Happy Friday Everybody! This week we're spotlighting three patient stories: an ALD patient full of optimism and love, a beauty pageant contestant with a noble goal, and a woman with…
According to a story from biotechconnectionbay.org, medical researchers are beginning to more closely investigate that possibilities that drug repurposing, or using old drugs for treating different illnesses, could offer. While…
The phase 3 trial of the drug Inlyta for the treatment of patients with a high risk of recurrent renal cell carcinoma (kidney cancer) following nephrectomy (removal of a kidney)…
According to a story from statnews.com, a drug derived from substances originating in the cannabis plant may be nearing approval by the U.S. Food and Drug Administration. The drug is…
For many, being diagnosed with any disease – let alone a rare disease – is understandably devastating. Many have described managing their new lives as learning a new language or…
According to a story from the Lyme Disease Association, researchers from the University of Maryland have discovered at least part of the method by which the bacteria responsible for Lyme…
Researchers are arguing that the certain drugs, including the erectile dysfunction drug Viagra, could be used as cancer treatments, reports MedicalXpress. This theory is based on a range of pre-clinical…
A recent study, published in Nature Communications and reported on by the BBC, has discovered five genes that are linked to pulmonary arterial hypertension. Pulmonary arterial hypertension (PAH) is the…
The 2018 Mrs. Maine International Pageant will be so much more than a celebration of poise and beauty. It will also make history when Devan Demmons will proudly walk on…
The pharmaceutical company Lonza has just opened a new state-of-the-art manufacturing facility to produce cell and gene therapies. You can find the full press release here, on Lonza’s website.…
Content warning: discussion of ableism and eugenics A woman is suing the Japanese government over her forced sterilisation four decades ago. This is the first case to be brought against…
According to a story from Summit Medical Group, a recent study indicates that survivors of testicular cancer may have a greater risk for heart disease. Compared to many types of…
Scientists are investigating whether delaying the onset of epilepsy in very young children could reduce or prevent other neurological conditions such as learning difficulties and autism, reports Medical Xpress. This…
A press release from Applied Genetic Technologies Corporation, which can be found in full at GlobeNewswire, has announced that enrolment for a phase 1/2 clinical study has been completed. The…
Women’s* biology and symptoms are often misunderstood in medicine, which leads to difficulties in diagnosis and treatment. Maya Dunsenbery, a journalist suffering from rheumatoid arthritis (RA), recently wrote a book,…
A young woman in Cambridgeshire received a trailblazing double lung transplant. Now she’s started a Kickstarter campaign to publish a book to help other people in similar situations, their friends…
A drug called Kineret has been approved by the European Commission in 28 European countries for the treatment of both adult-onset and juvenile-onset Still’s disease, reports Check Orphan. Still’s disease…
In an $8.7 billion agreement, Swiss drugmaker Novartis recently acquired AveXis. The company moved in such a way in order to acquire a developmental therapy for spinal muscular atrophy. The…
The University of Maryland has just published a press release after a researcher working at the university made several new discoveries about the bacteria that causes Lyme disease. Lyme disease…
According to a story from stv.tv, 14-year-old Kira Noble has been fighting against neuroblastoma for around over four years. She first began to realize that something was wrong when her…
According to a story from wired.com, a new genomics marketplace called Helix will soon start selling genetic tests directly to consumers. These tests are the same ones that doctors use,…
According to a story from globenewswire.com, the pharmaceutical companies Ultragenyx and Kyowa Kirin recently issued an announcement that the U.S. FDA has granted approval to their new treatment Crysvita (burosumab-twza).…
Pfizer has just begun a medical trial for a potential gene therapy treatment for Duchenne muscular dystrophy, and the first patient has been dosed. Click here to read the original…
According to a story from news.vanderbilt.edu, Charlotte Haffner has been working hard to advocating on behalf of amyloidosis patients. She recently underwent a heart transplant and stem cell transplant in…
According to a story from prweb.com, a possible cause of Meniere's disease may have been discovered by Dr. Michael Burcon, who has a dedicated a significant portion of his…
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