According to a story from ibtimes.co.uk, Sue Cox, a 65 year old Welsh woman from Cwmbran, has sought alternative methods for dealing with the worst symptoms of her multiple sclerosis.…
Reported by Strait Times, it was announced by Ministry of Health last week that there may be a potential fund developed to help children who suffer not only from a…
Tomorrow is Moebius Syndrome Awareness Day! Moebius Syndrome Awareness is celebrated globally each year - with the goal of raising awareness about this rare condition and to educate the many…
On January 17th, Parent Project Muscular Dystrophy announced that the first patient had been treated with a new gene therapy. The therapy developed specifically for Duchenne muscular dystrophy is known as…
According to an article from rdmag.com, a new form of treatment could allow for organ tissue to regrow to a normal level in patients with conditions in which organs are…
The gene therapy development company, AveXis, Incorporation, just announced that they will be expanding their clinical trial development program for the potential gene therapy treatment: AVXS-101, reported Globe News Wire.…
According to BBC News, a new universal blood test is receiving a lot of buzz due to it's potential to detect early stages of cancer. A research team at John…
The Driscoll family is left devastated and shocked after receiving a letter from social services that states the government could be taking their daughter, who is suffering from Rett syndrome,…
Potentially good news arrived for patients with hereditary TTR amyloidosis, as the treatment drug inotersen received it's New Drug Application approval and will go into review by the U.S. Food…
According to an article from PRNewswire, the drug MVASI (biosimilar bevacizumab) was just granted marketing authorization by the European Commission. Developed by Amgen and Allergan, this treatment has been approved…
According to an article from bioportfolio.com, the pharmaceutical company Ophthotech announced that the first of its patients are being enrolled in its Phase 2b clinical trial. This trial is meant…
According to a story from Drug Discovery & Development, The European Commission announced its approval of marketing certification for OCREVUS, a treatment for relapsing types of Multiple Sclerosis (MS). The…
19-year-old Jonathan Inkin created a "20-strong" bucket list with intention to cross them all off before his birthday. Thanks to the help of celebrity Toff (Georgia Toffolo), the winner of…
Tiffany and Caleb isn't your typical engaged couple. They are passionately in love and excited for their wedding, but their romance could literally end any moment. NBC 5 Chicago reported…
Reported by Fox 2, Anthony Anzell doesn’t let his rare genetic disease hold him back. Anthony is an extreme athlete who just swam 19 miles, the entire length of Torch…
Even though most in the medical field suggest that people think about their wishes as to how to handle end-of-life decisions, and complete the paperwork to be sure their wishes…
The Hempel family decided to take action against Vtesse and Sucampo Phamaceuticals who allegedly stole and sold their private information for profit, reported Forbes. The Hempel family has two twin…
Even after the third denial from the U.S. FDA, Food and Drug Administration, PTC Therapeutics Incorporation will not stop fighting for the drug Translarna that they believe will help patients…
A team of scientists recently developed an electronic nose that detects Crohn’s disease and ulcerative colitis. Continue reading below, or follow the original story to learn more about this intriguing…
The Wahlstrom family of four, is getting a miraculous gift to help care for their two children suffering from Batten disease, reported CBS Minnesota. With the love of their local…
The FDA, US Food and Drug Administration, unanimously agreed upon the recommendation for a new gene therapy that treats a rare form of blindness, reported ScienceNordic. Spark Therapeutics, a biotech…
There is potential for a new treatment for Duchenne muscular dystrophy. Duchenne muscular dystrophy (DMD) is a genetic disorder characterized by progressive muscle degeneration and weakness.To learn more about this…
TGIF, Patient Worthians! This week, kids went to bed wearing inside out pajamas and wishing for snow. Their wishes came true-- and so did the wishes of many rare disease…
According to an article from One News Page, the biopharmaceutical company Motif Bio was generously presented with an award from the Cystic Fibrosis Foundation. The award came in the form…
If you live near Pompano Beach in Florida, the Water Balloon Bulls-eye charity event is not to be missed, reported Sun Sentinel. The event is focused on raising money, as…
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