According to a story from EurekAlert! an international team of scientific researchers have made an unusual discovery. The team found in the course of their studies that dietary supplementation with…
China has been making waves lately, improving its efforts to efficiently and effectively provide healthcare for its nearly 1.5 billion population. “Health is a prerequisite for people's all-round development and…
Happy Thursday! Today, we're highlighting stories on three patients facing different struggles: a professor, a Jeopardy host, and a man from New Jersey. We also have an article about a…
Tannaz Motevalli Tannaz Motevalli is the Exhibition Coordinator at the National Library of Medicine, an artist, a researcher, and a writer. She also lives with cystic fibrosis (CF). Experiencing fewer…
According to a story from Pancreatic Cancer Action Network, there are a wide variety of different treatment approaches for cancer; however, the effectiveness of these treatments so far has been…
In honor of its 30th anniversary, the National Organization for Rare Disorders (NORD) has announced ten new grants as part of its Rare Disease Research Grant Program! NORD is the…
According to a story from BioSpace, on June 7th, 2019, Londyn Wright became the first baby in the US to receive Zolgensma, a recently approved gene therapy treatment for the…
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According to a recent article in MedicalXpress, the story begins fifty years ago with the grim statistics that a child with acute lymphoblastic leukemia (ALL) would not survive longer than…
According to a story from BioPortfolio, the biopharmaceutical company AstraZeneca recently announced the release of positive results from a phase 3b clinical trial. This trial was testing the safety and…
According to a story from Pulmonary Hypertension News, a recent study has found that lapses in treatment adherence can result in serious side effects for pulmonary arterial hypertension (PAH) patients…
According to a story from princetoninfo.com, Sara Cooper was diagnosed last November with amyotrophic lateral sclerosis. Sara has had an active career as an event planner, marketing consultant, and real…
According to a story from Global News, Charleigh, the three year old daughter of Trevor Pollack and Jori Fales, was recently diagnosed with CLN2 Batten disease, which is a rare…
According to a story from Cancer Therapy Advisor, a recent study published in the journal Cancer Medicine indicated that chronic lymphocytic leukemia (CLL) patients who dealt with adverse events during treatment…
According to a press release from the French biotechnology company Inventiva, the company has completed recruitment for a phase 2 clinical trial evaluating its experimental mucopolysaccharidosis VI drug, odiparcil. About…
Von Willebrand disease is the most common inherited blood clotting disorder that affects humans. The disorder can also be acquired. Although it is considered common, the majority of cases do…
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Social media, and especially Facebook, have become our “windows to the world”. According to a recent article that appeared in The Michigan Public Health News Center, scientists are using…
According to a story from Bioscience Today, amyotrophic lateral sclerosis (ALS), also known as Lou Gehrig's disease or motor neurone disease, has continued to be a mysterious disease for the…
According to a story from Charcot-Marie-Tooth News, a recent study was conducted that compared the presentation of symptoms between two different variants of Charcot-Marie-Tooth disease (CMT): CMT4B1 and CMT4B2. The…
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The blood-brain barrier is a “gatekeeper” that prevents toxins and foreign matter in the bloodstream from traveling to the brain. Check Orphan recently carried an article that had been…
According to a publication from Pharmaceutical Technology, California-based Eiger Biopharmaceuticals is preparing to submit a New Drug Application (NDA) to the Food and Drug Administration (FDA) for their experimental progeria…
According to a publication from Stat, researchers from the University of Michigan-led Genes for Good program have recruited over 20,000 Americans through its smartphone app. Participants complete questionnaires on the…
According to a story from drugs.com, the pharmaceutical company Merck recently announced that the US Food and Drug Administration (FDA) has approved its drug pembrolizumab (marketed as Keytruda) as a…
Jane Biehl Jane Biehl has worked as a professor, rehabilitation counselor, and a librarian. She holds three different degrees, and spreads her knowledge through freelance writing. She also has a…
According to a story from marketscreener.com, the biotechnology company Roche recently announced the results from a company sponsored phase 3 clinical trial that compared the safety and efficacy of rituximab…
It is 2019, and minority populations still account for fewer than 10% of clinical trial participants. Two decades ago, the "NIH Policy and Guidelines on the Inclusion of Women and…
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