According to Myasthenia Gravis News, CAAR T-cell therapy may be a viable treatment option for those with myasthenia gravis. Researchers from the University of Pennsylvania, Yale Medical School, and Cabaletta…
In a recent press release, biotechnology company Sarepta Therapeutics announced positive findings from their clinical trial studying SRP-9003 as a treatment for limb-girdle muscular dystrophy (LGMD) type 2E. This…
You have a number of different cells throughout your body, all of which perform different functions or provide support. One extremely interesting type are astrocytes, star-shaped glial cells that…
During this time of COVID-19, many people have some general information about COvID-19 including the knowledge that individuals over 65 years of age are at higher risk of contracting…
Over the last few years, I've heard the refrain that my health - oddly - starts in my gut. So whenever I got sick, someone would advise me to…
Plakous Therapeutics released a press release to announce that Protego-PD™, their therapy for infants with necrotizing enterocolitis (NEC), received both the Orphan Drug and Rare Pediatric Disease designations from the FDA. There are…
According to Parkinson's News Today, the FDA is reviewing Gocovri as a potential treatment for "off episodes" in patients with Parkinson's disease who are already taking levodopa. "Off episodes"…
According to a story from ajmc.com, a recent study found that a new combination treatment for systemic amyloid light-chain (AL) amyloidosis is more effective than the current standard treatment. The…
By Jodee Redmond, In the Cloud Copy The work of a pediatric oncologist isn’t for the faint of heart. All their patients are children, and the outcome isn’t always good.…
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