According to a Town News press release, Sound Pharmaceuticals, a biopharmaceutical company based in Seattle, received FDA approval for their Phase 3 clinical trial on SPI-1005. The trial, STOPMD-3,…
Growing up, my family and I faithfully watched Survivor each week. Although my parents stopped watching a few years back, settling in every Wednesday during the season is somewhat of a…
According to a story from PR Newswire, CureDuchenne Ventures has recently announced the initiation of its CureDuchenne Ventures 2020 Pitch Contest. This marks the first time that the contest has…
According to a story from BioSpace, the radiopharmaceutical company Clarity Pharmaceuticals has recently announced that the US Food and Drug Administration (FDA) has granted Rare Pediatric Disease designation to its…
Last night, I texted my mom to ask what blood type I was. "Type A, I think? I'll have to check. Why?" she texted back. Well, I had just read…
As much as you and I have tried to keep up on COVID-19 news, the information changes every day. Although about 80% of cases are asymptomatic or mild to…
According to a story from BioSpace, the biopharmaceutical company MacroGenics, Inc. has just announced that the US Food and Drug Administration (FDA) has given Orphan Drug designation to the company's…
In a press release from Eli Lilly and Company, the company has announced recently that the US Food and Drug Administration (FDA) has approved the supplemental Biologics License Application (BLA)…
Acadia Pharmaceuticals recently released the results of their Phase 3 trial of Nuplazid, a treatment for the psychosis that Parkinson's disease patients experience. This medication has been approved since 2016,…
La investigación genética es un campo floreciente y emocionante. Con el descubrimiento de nuevas mutaciones y variantes genéticas se llega a una comprensión más profunda de las enfermedades raras y…
Gut bacteria has been connected to a number of conditions: depression, diabetes, and now Parkinson's disease. A study published in Annals of Neurology has shown that gut bacteria is linked…
June marks the start of Aphasia Awareness Month, designed to educate many on aphasia: causes, long-term affects, and the lives of those living with this condition. But, as the University…
According to News Medical, a recent international study designed to understand Lesch-Nyhan syndrome and its potential treatments discovered something intriguing: biochemical changes in the skin, cerebrospinal fluid, and urine. Now,…
A recent study that utilized the COVID-19 Global Rheumatology Alliance registry has evaluated the risks that the novel coronavirus brings to those with lupus and other rheumatic diseases, as reported…
According to a story from Multiple Sclerosis News Today, the drug company Bristol-Myers Squibb recently announced that its drug ozanimod (marketed as Zeposia) is now available for public use in…
According to Disability Horizons, an extremely talented filmmaker with muscular dystrophy recently won an Award of Recognition from The Best Shorts Film Competition. Stephanie Castelete-Tyrrell's film, entitled Muscle Warriors, documents…
Stacey Saiontz is many things: a worker, a wife, a mother. But right now, she is concerned. As an allergy parent, or a parent whose child has severe food…
In a press release on PRWeb, the Southwest Eye Institute explains how Dr. Ahmed Soliman recently performed a Bowman layer transplant to treat keratoconus. This unique and minimally-invasive procedure, which…
PharmaEssentia Corporation, a biopharmaceutical company located in Burlington, Massachusetts, has recently seen their Biologics License Application (BLA) approved by the FDA. This application was submitted for ropeginterferon alfa-2b, a treatment…
Se realizó un estudio que podría ser el rituximab puede ser preferible a los tratamientos tradicionales para la miastenia gravis. También concluyó que el tiuximab es el más efectivo si…
It has been nearly 3 months for Vonny LeClerc, a 32-year-old journalist from Glasgow, Scotland. Nearly 3 months of extreme fatigue, joint pain, body aches, chest pain, intermittent fevers and…
Exercising has many physical and emotional benefits. It can manage blood sugar levels, improve your mood, assist with weight loss, or even strengthen your memory. Endurance training, specifically, benefits tissue…
According to a story from PR Newswire, the National Organization for Rare Disorders (NORD) has recently awarded a total of eleven new grant awards that will help fund essential research…
According to a story from EurekAlert!, a recent international study is utilizing data from 45 patients to describe a mostly unknown new rare genetic disorder. The researchers are recommending that…
NAMI, the nation’s foremost agency for mental health, defines depression as “more than just feeling sad” or just a “rough patch” in our lives. Doctor Susan Noonan reported on…
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