Stem Cells Could Cure the Most Common Cause of Irreversible Blindness 
source: pixabay.com

Stem Cells Could Cure the Most Common Cause of Irreversible Blindness 

As reported in Medical Xpress; Fight for Sight, a charity in the UK dedicated to vision, has an exciting announcement for people with macular diseases: they have just granted funding…

Continue Reading Stem Cells Could Cure the Most Common Cause of Irreversible Blindness 
ICYMI: EC Approves OXLUMO for Patients with Primary Hyperoxaluria Type 1
JillWellington / Pixabay

ICYMI: EC Approves OXLUMO for Patients with Primary Hyperoxaluria Type 1

  In late November, RNAi therapeutics company Alnylam Pharmaceuticals ("Alnylam") announced that its therapy OXLUMO (Lumasiran) received approval from the European Commission (EC) for both pediatric and adult patients with…

Continue Reading ICYMI: EC Approves OXLUMO for Patients with Primary Hyperoxaluria Type 1
Love, Work, Progress, and Community in Facioscapulohumeral Muscular Dystrophy
source: pixabay.com

Love, Work, Progress, and Community in Facioscapulohumeral Muscular Dystrophy

Colette Wheeler is one of four siblings, and although each had only a 50/50 chance of inheriting the genetic mutation that leads to facioscapulohumeral muscular dystrophy (FSHD), all of them…

Continue Reading Love, Work, Progress, and Community in Facioscapulohumeral Muscular Dystrophy