May is recognized annually as Cystic Fibrosis (CF) Awareness Month. Each year, this rare disease community comes together in order to help spread awareness about cystic fibrosis among the general…
When Shellye Horowitz was younger, she had a clear link to the rare disease community: her father. He had hemophilia and, much like many patients, relied on blood clotting factor…
Researchers at the University of Houston have been investigating lupus nephritis and discovered that there are race-specific urinary biomarkers. Hugh Roy and his team have found that there are specific…
Bronchiectasis News covers a potentially beneficial treatment for patients with bronchiectasis: bubble-positive expiratory pressure, or Bubble-PEP. These devices help clear mucus from the lungs. Although other forms of airway clearance…
According to BioTechniques, American researchers have taken a new, hands-on approach to learning more about cytomegalovirus-induced microcephaly. Although cytomegalovirus has been linked to microcephaly, the topic is somewhat under researched.…
A total of one hundred vaccines are being developed by researchers, drug manufacturers, and governments worldwide in an effort to stem the tide of the COVID-19 virus. Reuters Newswire reports…
By Danielle Bradshaw from In The Cloud Copy Seventeen-year-old Marissa, from Clinton Township, Michigan, might be what most would consider a model student. She earns good grades and she really enjoys…
According to a story from Xconomy, the drug company PTC Therapeutics has come to an agreement that will allow it to acquire Censa Pharmaceuticals and its lead product candidate. This…
A team of researchers recently clarified how cellular mechanisms work in the treatment of Krabbe disease. Previously, researchers believed that bone marrow transplants assisted in providing positive patient outcomes through…
ProMIS Neurosciences is a biotechnology company that works specifically with antibody treatments, and they have recently developed intrabodies for the treatment of amyotrophic lateral sclerosis (ALS). This same therapy has…
It is acknowledged in the medical community that clumps of misfolded tau proteins and amyloid-β are markers of Alzheimer’s disease. The evidence presented in recent article in Nature, shows that…
According to UIC Today, Jessica Lechuga became immersed within the rare disease community when she was still a teenager. That's because, at age 17, Jessica gave birth to her daughter…
According to WMC5, a research study out of Cleveland, OH, has been testing the impact of robotic exoskeletons on movement for patients with multiple sclerosis. For Kathy Miska, this is…
Según un comunicado de prensa en Global Newswire, la compañía biofarmacéutica MediciNova recibió un Aviso de concesión para una solicitud de patente para MN-166, que podría usarse para tratar el…
According to a recent article in BioMed Central, an international task force formed in 2018 created guidelines for the treatment of juvenile idiopathic arthritis (JIA). Treatment targets were identified…
Patients with hemophilia may experience sudden bleeding, joint pain and inflammation, and deep bruising. But according to Hemophilia News, two proteins may be the cause. Researchers found that patients…
Continued From Part Two Written by Payel Bhattacharya I hope for aid from the government to cover the high cost of subsequent medicines including anti-rejection medicines, radiological and lab…
COVID-19 has rapidly spread across the globe. With nearly 2.7 million diagnosed cases, the medical field is overworked. As a result, many hospitals and doctors are experiencing a lack…
Hello! We hope that within all this chaos, you're still able to enjoy some parts of spring. Today, we have a story about kids with disabilities who are affected by…
Kubota Vision, a subsidiary of Kubota Pharmaceutical Holdings, has recently finished enrollment in the third phase of their emixustat hydrochloride (emixustat) trial. Emixustat hydrochloride is a treatment for Stargardt disease…
Merck and AstraZeneca recently announced that Lynparza improved overall survival in the lives of males with advanced prostate cancer who had been treated previously. The drug out-performed two other antiandrogen…
Of course, parents are not used to taking on the role of educator. Many are still working full time jobs at home. That, in addition to the normal household chores,…
According to Angelman Syndrome News, researchers used rat models of Angelman syndrome to test gene editing as a potential therapy. They found that CRISPR technology deleted the defective UBE3A gene. However, rats…
As COVID-19 continues to spread, and the length of our lockdowns increases, many patients with rare diseases and their families are wondering what comes next. How will you receive treatment?…
Recientemente, el Dr. Ian Winburn de Pfizer se sentó con Europabio para una entrevista en honor del Día Mundial de la Hemofilia, que acaba de ocurrir el 17 de…
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