A glioblastoma diagnosis can be devastating. Currently, the 5-year survival rate is under 10%. This highly malignant cancer, which forms in the brain and spinal cord, is also somewhat difficult…
Welcome to the Rare Classroom, a new series from Patient Worthy. Rare Classroom is designed for the curious reader who wants to get informed on some of the rarest, most…
Grant and award programs can be crucial in spurring therapeutic discovery and development. According to News Medical, this is what the Follicular Lymphoma Foundation (FLF) aims to do with its…
Recently, Chain Drug Review reported that the FDA had approved a generic form of colchicine pills (normally prescribed as Mitigare, Colcrys, or Gloperba) for the treatment of familial Mediterranean fever (FMF).…
According to a recent article, the drug dovitinib has been submitted to the FDA for pre-marketing approval as a third-line therapy for patients diagnosed with renal cell carcinoma (RCC). Renal…
According to the Cancer Network, a CAR T-cell therapy called C-CAR039 recently earned both Fast Track and Regenerative Medicine Advanced Therapy (RMAT) designations from the U.S. Food and Drug Administration.…
Compassion [kuhm-pash-uhn] noun A feeling of deep sympathy and sorrow for another who is stricken by misfortune, accompanied by a strong desire to alleviate the suffering. Compassion Corner is a…
It's January -- do you know what that means? That's right - it's National Glaucoma Awareness Month! According to the Richmond Register, glaucoma diagnoses are rising on a national level.…
On January 12, 2022, posts shared on Facebook and Instagram announced the passing of 15-year-old Adalia Rose Williams. A Youtube and Facebook star, Adalia had over 16 million followers collectively.…
Crohn’s disease causes inflammation throughout the digestive tract. But what factors influence the severity of this inflammation? Medical XPress describes how a study out of Case Western Reserve University discovered…
There are many terms that were once widely used which held offensive origins and meanings towards certain groups. Now, in a more socially conscious society, we are rightfully abandoning these…
According to a recent article from MedPage Today, the results from a small prospective study show that sequential radiotherapy (RT) is successful in delaying systemic therapy for oligometastatic renal cell…
In the past, there have been little to no concrete studies evaluating the relationship between hereditary angioedema (HAE) and cancer risk. However, researchers questioned whether some sort of relationship could…
According to a recent article, a new stem-cell-based gene therapy is showing promising results for treating beta (β)-thalassemia in a phase 1 clinical trial. Beta Thalassemia Beta thalassemia is a…
How does long-term non-steroidal anti-inflammatory drug (NSAID) use influence health? Do NSAIDS used by older adults influence the development of any other conditions or adverse reactions? According to the Nephrology…
Biogen Inc. recently announced data that included extended results from its earlier Phase 3b NOVA study on the administration of natalizumab and the evaluation of the drugs Tysabri® and Vumerity. …
What if researchers could change DNA processes within brain tumors to improve overall survival rates and patient outcomes? According to Medical XPress, researchers found that L-methylfolate, in conjunction with the…
Newborn screening (NBS) is a public health service within the United States through which babies are screened for medical conditions that otherwise wouldn't be apparent at birth. Many of the…
Today, follow along on a case study exploration to see how a 52-year-old woman finally received a diagnosis of stiff person syndrome (SPS), a rare neurological disorder. According to the…
Is there a relationship between increased sun exposure and breast cancer risk? At first glance, you might think, “Sure. Sun exposure probably increases the risk.” However, according to an article…
According to a recent article, Apellis Pharmaceuticals and Swedish Orphan Biovitrum AB recently announced the European Commission (EU) has approved Aspaveli to treat adults with paroxysmal nocturnal hemoglobinuria (PNH). Paroxysmal…
It’s no secret that stress can be both psychologically and physically damaging. But how does stress influence the way that our bodies respond to certain conditions? According to Medical XPress,…
When she was born, Savannha Aretino was diagnosed with hypophosphatasia, a rare genetic disorder characterized by bone and teeth development abnormalities. Now, twenty-three years later, Savannha is working to not…
According to a recent article, a study shows that treatment with gene therapy reduces the need for patients with non-β0/ β0 genotype Beta-thalassemia (β-thalassemia)to get transfusions. Beta-thalassemia (β-thalassemia) Beta thalassemia…
The Pitt Hopkins Family Conference & Scientific Symposium (PHRF Conference) will be held June 23rd through June 25th, 2022 in Chicago to raise awareness and share research updates for Pitt…
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