Welcome to Study of the Week from Patient Worthy. In this segment, we select a study we posted about from the previous week that we think is of particular interest…
Due to varied periods of decline among patients, previous research indicates that it is difficult to develop treatment options for patients who have relapsed DLBCL. This holds true especially when…
Patrick Freyne recently interviewed three people with myalgic encephalomyelitis (ME) for his column in the Irish Times. Patrick describes the circumstances behind the first known cases of the ME…
According to a late September 2022 news release from biopharmaceutical company AEON Biopharma, Inc., positive topline data is available from a clinical trial evaluating ABP-450 for patients with cervical…
On October 20, 2022, the Rare Disease Legislative Advocates (RDLA) hosted their monthly webinar. These webinar help provide updates to the rare disease community on legislation and other policy initiatives…
Three of Edith Lemay and Sebastien Pelletier’s four children were diagnosed with retinitis pigmentosa, an untreatable genetic condition. The parents were told their children would eventually be blind. In trying…
Master Chef Christine Ha of Dublin is coping with the fact that an accurate diagnosis years earlier would have prevented her blindness. Christine now spends a great deal of time…
In 2001, dystonia totally changed my life. I put together a video that shares my 20+ year pictorial journey with dystonia, chronic pain, and overcoming anxiety, depression, and morbid obesity…
Did you know that bone mass accrual and bone mineral density depend highly on puberty? Because of this, puberty delays or interruptions can negatively affect bone mineral density or cause…
Several years ago, Laura Evans of Clydebank, Scotland received devastating news from her doctor that she only had two years to live. Laura had been diagnosed with a type of…
Compassion [kuhm-pash-uhn] noun A feeling of deep sympathy and sorrow for another who is stricken by misfortune, accompanied by a strong desire to alleviate the suffering. Compassion Corner is a…
According to a story from AJMC, only a small number of cases of hypoparathyroidism have been reported alongside systemic lupus erythematosus (SLE). However, despite the overall rarity of the scenario,…
In an October 13, 2022 news release from biotechnology company INOVIO, the company shared that positive interim data was available from a Phase 1/2 study. Within the study, researchers…
It’s no secret that excess alcohol consumption can result in numerous adverse health effects. According to an article in the Pharmacy Times, researchers sought to understand how excess alcohol…
Currently, treatment options for Williams syndrome are considered symptomatic; they treat symptoms of the condition, but not the underlying cause. There are no treatments or cures addressing the underlying genetic…
For most of my 21 years with chronic pain and other symptoms from dystonia, a neurological movement disorder, I viewed it as a curse; an evil intruder that ruined my life.…
Although paroxysmal supraventricular tachycardia (PSVT) may not be a common household name, it is experienced by five hundred Americans with over fifty thousand patients visiting hospitals for treatment in…
According to an article in GastroEndo News, first published in Clinical Oncology News, the U.S. Food and Drug Administration (FDA) recently approved a combination of durvalumab and gemcitabine plus…
What is the best therapeutic option for individuals with atrial fibrillation (AF or AFib) and chronic kidney disease (CKD)? Currently, doctors typically recommend direct oral anticoagulants (DOACs) to patients with…
Enzyme replacement therapy (ERT) is an approved treatment strategy for those with Pompe disease. It involves providing patients with alpha-glucosidase, which helps to break down glycogen. In addition to reducing…
In 2019, Takeda Pharmaceutical Company experienced some manufacturing and production issues related to its product Natpara, a treatment option for individuals with hypoparathyroidism. The product was recalled in the…
Welcome to Study of the Week from Patient Worthy. In this segment, we select a study we posted about from the previous week that we think is of particular interest…
A team of researchers at Israel’s Weizmann Science Institute and California University in San Diego linked fungi to approximately 35 cancers. They created a pan-cancer mycobiome atlas exposing new…
In late September 2022, Healio reported that the U.S. Food and Drug Administration (FDA) approved bevacizumab-adcd (Vegzelma), a biosimilar of Genentech’s bevacizumab (Avastin). The approval of biosimilars such as…
Each year, an estimated 2.9 million cases of cholera are reported across the globe. Caused by Vibrio cholerae (V. cholerae) bacteria, cholera can cause shock, dehydration, and even death.…
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