Jessica Lynn has an educational background in writing and marketing. She firmly believes in the power of writing in amplifying voices, and looks forward to doing so for the rare disease community.
The U.S. Food and Drug Administration (FDA) runs a number of programs designed to facilitate research and drug development for serious conditions. One such program is the Fast Track program;…
According to Multiple Sclerosis News Today, the European Commission (EC) recently approved PONVORY (ponesimod) for the treatment of adult patients with relapsing and remitting (R/R) or active secondary progressive (SP)…
In 2020, Dr. Paul Orchard, a pediatric blood and bone marrow transplant physician at M Health Fairview University of Minnesota Masonic Children’s Hospital, attended a medical conference that would change…
Currently, there are a number of potential treatment options for patients with multiple myeloma: immunomodulators, chemotherapy, HDAC inhibitors, steroids, and proteasome inhibitors. But according to Medical XPress, Peter Mac scientists…
According to Medical XPress, researchers from the Cerebrovascular Surgery and Interventions Center at Boston Children's Hospital recently developed a new test that can benefit patients with Moyamoya disease. This rare…
In many cases, therapies for patients with rare disease are first tested or developed in either 2D cell cultures or in animal models, such as fruit flies, mice, or zebrafish.…
The amount of marijuana users in the world is steadily growing. While some people use marijuana to relax, others use medical cannabis for chronic pain, rare epilepsies, glaucoma, multiple sclerosis…
Our livers play a huge role in our health. The liver regulates chemicals in the blood, filters toxins and wastes out of the body, breaks down fat, and even plays…
In a news release from early May 2021, biopharmaceutical company Bold Therapeutics ("Bold") shared that its treatment BOLD-100 received Orphan Drug designation for the treatment of patients with gastric…
Nobody knew how much of an impact COVID-19 would have when it first appeared on the scene. Now, as of May 20, 2021, the novel coronavirus pandemic has led to…
In a news release from May 19, 2021, startup biotechnology company GeneTx Biotherapeutics LLC ("GeneTx") and biopharmaceutical company Ultragenyx Pharmaceutical Inc. ("Ultragenyx") shared that the pair received Health Canada clearance…
In a news release from May 18, 2021, biopharmaceutical company Catalyst Biosciences, Inc. ("Catalyst") shared that the first patient was dosed in the Phase 1/2 MAA-202 clinical trial. During…
According to corporate news shared on Street Insider, biopharmaceutical company BridgeBio Pharma, Inc. ("BridgeBio") is making ground with its AAV5 gene therapy, BBP-631. Recently, the FDA granted Fast Track designation…
The first time I got stung by a wasp, my knee swelled up to nearly 4x its size. While my allergy is more frustrating than fatal, I know that I…
Clinical trials are extremely beneficial in learning how new and burgeoning treatment options can benefit patients. At the same time, these trials also offer insight into where treatments may not…
Sometimes, in the midst of performing medical research, researchers may discover an association between two conditions. According to Lambert Eaton News, University of Turin researchers recently determined a link between…
Unfortunately, the COVID-19 pandemic has sidelined many events, fundraisers, and other opportunities over the last 14 months. But the pandemic won't stop the Kidney Foundation of Canada from holding…
This year, the American Academy of Neurology (AAN) Annual Meeting took place virtually from April 17-22, 2021. During the meeting, a variety of stakeholders discussed new treatments and research…
Currently, there is no cure for mesothelioma, and many treatment options revolve around surgery, radiation, or therapy. But could targeted treatment and precision oncology provide better patient outcomes? According to…
From April 23 to 25, 2021, the American Academy of Dermatology (AAD) held their 2021 Virtual Meeting Experience (AAD VMX 2021). During the meeting, a variety of dermatology stakeholders discussed…
Have you ever thought about whether measuring caffeine levels could give you insight into disease progression? Well according to Parkinson's News Today, researchers have discovered a potential link between…
For many patients with diffuse large B-cell lymphoma (DLBCL), one first-line treatment is rituximab, cyclophosphamide, doxorubicin, vincristine, and prednisone (R-CHOP). However, even aggressive chemotherapy is not always enough for patients…
Poly ADP ribose polymerase (PARP) inhibitors are targeted cancer therapies which block PARP, an enzyme. Normally, PARP plays a role in DNA repair. Thus, inhibiting PARP prevents cancer cells from…
Over the last 15~ months, the world has grappled with the impact of COVID-19, a novel coronavirus. Altogether, COVID-19 has led to over 156 million million cases with an associated…
There are two types of osteosarcoma, a rare bone cancer: localized or metastasized. If the cancer is localized, or in one area, the 5-year survival rate sits around 70-75%. However,…
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