According to a story from EurekAlert!, scientists from UCLA have developed a new method of delivery for gene therapies called nanospears. These structures could allow for more accurate and precise…
According to a story from Teen Vogue, Midnight Sun, a new film starring Bella Thorne, is slated for release on March 22nd, 2018, is a romantic drama whose central character,…
According to a story from BioSpace, the U.S. Food and Drug Administration has given Fast Track designation for nintedanib, which is undergoing testing for the treatment of systemic sclerosis with…
According to a story from raredr.com, The U.S. Food and Drug Administration (FDA) has recently approved Hizentra as a maintenance therapy for patients with chronic inflammatory demyelinating polyneuropathy. Hizentra is…
According to a story from raredr.com, the FDA had to order the cessation of Phase II/III trials for the microdystrophin transfer therapy SGT-001, which was in development for the treatment…
According to a story from BioPortfolio, a recent study claims the Morgellons disease, a condition that has been shrouded in confusion and controversy, is not a delusion as some prior…
According to a story from LiveScience, nine dentists and dental workers in the state of Virginia have been diagnosed with idiopathic pulmonary fibrosis, a rare and dangerous lung disease. All…
According to a story from The Globe and Mail, doctors were baffled after four young women who had a deadly and rare type of ovarian cancer were saved with an…
According to a story from Central Texas News Now, a four-year-old girl with an extremely rare form of mitochondrial disease got her wish to see snow. The girl, Scarlett Landry,…
According to an article from Neuroscience News, a new discovery may help explain why men are less likely to develop multiple sclerosis than women. The new information may also be…
According to a story from drugs.com, kids and teenagers with chronic kidney disease (CKD) may develop problems with learning and cognition, a new study suggests. Researchers emphasize that patients on…
According to a story from 13abc.com, a family is working to spread awareness about Batten disease after second grader, Charles Klein was diagnosed with the condition. The disease has no…
According to a story from The Independent, Britain's disability welfare program is coming under fire for its Personal Independent Payment (PIP) assessments. Statistical measures suggest that these assessments are taking…
According to an article from Medical Xpress, a recent study suggests that an anti-cancer drug commonly used to treat leukemia may be effective in treating a rare form of ovarian…
According to a story from Charcot-Marie-Tooth Disease News, the U.S. Food and Drug Administration (FDA), under the leadership of commissioner Scott Gottlieb, has begun to change clinical trials by accepting…
According to a story from Medical Xpress, the addition of crizotinib with radiation therapy could help reduce hearing loss associated with the treatment in patients with neurofibromatosis II. Crizotinib is…
According to a story from the Vancouver Sun, 11-year-old Jaylene Prime from British Columbia was able to obtain access to a critical treatment for her juvenile idiopathic arthritis. The drug,…
According to a story from wired.com, Stephen Hawking, one of the most famous physicists on the planet, passed away on Wednesday, March 14th, 2018. He was 76 years old. His…
According to a story from All4Women, Nicole Capper, crowned Mrs. South Africa, is planning to summit Mt. Everest, the highest mountain peak on the planet, in order to help promote…
According to a story from markets.financialcontent.com, approximately 300 Parkinson's disease advocates and disease experts are slated to meet in Washington, DC for the Parkinson's Policy Forum. This year, the event…
Rare disease patients remain one of the most underserved medical populations, and they often have to deal with debilitating symptoms or complications that can make daily life difficult. For example,…
According to a story from macleans.ca, after beginning to develop problems with mobility such as climbing stairs, Julie Mason of Montreal endured years of confusing tests before doctors were able…
According to a story from the Wall Street Journal, the U.S. healthcare system might be able to learn a thing or two from Netflix. A well understood aspect of healthcare…
CRISPR gene editing technology is still mostly in its infancy, but the new tool is already causing a lot of excitement, particularly in the treatment of genetically-linked diseases. A recent…
According to a story from PressReleasePoint, a new partnership has developed to generate artificial intelligence technology that will help diagnose people with a variety of rare diseases. The partnership consists…
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