UniQure Publishes Phase I/II Trial Results of AMT-060 Gene Therapy in Treating Hemophilia B
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UniQure Publishes Phase I/II Trial Results of AMT-060 Gene Therapy in Treating Hemophilia B

Pharmaceutical company and gene therapy leader, uniQure, published promising data from their current phase I/II trial testing out a gene therapy called AMT-060 in patients with serious cases of hemophilia B.…

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Editor’s Choice: Events on Events on Events! Help Raise Sjogren’s Awareness and BOS Awareness

Happy Friday Patient Worthians! April is Sjogren's Awareness Month! There was also a whole day dedicated to Bohring-Opitz Syndrome. The MDS Foundation has another upcoming event as well. Lastly, last month…

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Murder in the Royal Family: How Researchers Discovered Hemophilia in Queen Victoria’s Bloodline
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Murder in the Royal Family: How Researchers Discovered Hemophilia in Queen Victoria’s Bloodline

Royalty, murder, lots and lots of blood – sounds like elements from the plot of a Victorian-era thriller. Actually, this story comes straight from hemophilia history. Science Magazine published a…

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Editor’s Choice: Suddenly Sleepy and Beautifully Broken

Welcome back to Editor's Choice! This week we have an interesting take on Parkinson's treatment. We also have an empowering article from one of PW's rare disease contributors. We are all feeling the…

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Editor’s Choice: Pharma Freebies, Gadgets, & Nightmares

Happy Friday Patient Worthians! PW Contributor Nolan is back in our Video Series with his details on dystonia treatment. We also have some cool info on EDS gadgets! What do pharmaceutical companies mean…

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