According to NBC Right Now, the liver disease advocacy organization called The American Liver Foundation is launching an online platform designed to pair liver disease patients to clinical trials. The website,…
According to an article from VCU Massey Center's blog, a team of researchers from the VCU Massey Cancer Center have successfully discovered a pair of genes that could be essential for…
In an twist of fate, a brand new gene therapy for the treatment of Adrenoleukodystrophy (ALD) uses one of medicine's greatest nemesis, HIV, to treat this fatal genetic brain disease-- and…
According to a story from SMA News Today, a recent study has demonstrated that the parents of children with spinal muscular atrophy are often skeptical about enrolling their kids in…
Clinical trials of a potential gene therapy treatment for Duchenne muscular dystrophy (DMD) have been put on hold after concerns emerged about the safety of the procedure, reports Genetic Engineering…
According to a story from asianscientist.com, a group of Japanese researchers have managed to unearth a genetic mutation that is associated with progressive supranuclear palsy. The discovery is helping scientists…
Researchers at the University of South Florida have developed a blood test that may improve diagnosis for many diseases, including HIV and Lyme disease, reports EurekAlert. The new test uses…
An article from SRN News is reporting that a lot of people with familial hypercholesterolemia are going through life without getting the treatments that could help them, such as statins.…
A pre-clinical study investigating the effects of antioxidants on mitochondrial diseases has shown promising results, reports EurekAlert. Out of the seven antioxidants trialled, at least two (vitamin E and N-acetylcysteine)…
A gene therapy for Pompe disease is the first treatment of its kind to be clinically tested, reports Duke University. Researchers at the University, working with NCATS Therapeutics for Rare…
A team of researchers led by Prof. Michael N. Hall from Biozentrum, University of Basel, have discovered a tumour suppressor protein called LHPP. Their paper, published in the science journal…
Neurologists working at the NYU School of Medicine have developed a test that can identify some rare degenerative brain diseases, reports NYU Langone Health. Published in the Annals of Neurology…
A new drug being developed to treat Angelman syndrome (AS) has just been approved for ‘orphan drug’ status in the U.S., reports GlobeNewswire. The drug, called GTX-101, works by activating the…
According to a story from curetoday.com, a recent study indicated that many patients with uveal melanoma reported having unmet psychological and informational needs, particularly in the first several months after…
A new study conducted at Binghamton University demonstrated that pancreatic cancer cells can be killed with a dual thermal ablation process, which is the combination of freezing and heating, reports…
La Jolla Pharmaceutical recently announced a new clinical trial targeting thalassemia. The trial, described as pivotal, investigates a drug referred to as LJPC-401. The treatment is intended to help patients…
According to a story from medicalxpress.com, a recent study suggests that cognitive deficits that can occur as side effects of targeted brain cancer drugs could be successfully reversed with therapy.…
A recent story from The Independent is touting the results of a clinical trial that tested stem cells transplants for multiple sclerosis. The transplant appears to help "reset" the patient's…
The disease may be daunting, but it won't stop young, determined woman Ellis Kerton. According to LincolnshireLive, Ellis learned when she was 19-years-old that she was positive for Huntington's disease.…
According to an article from the Augusta Free Press, a research team from Vanderbilt University and the Virginia Tech Carilion Research Institute has successfully managed to uncover the manner in…
According to a story from mysunshinecoast.com.au, an international research team has uncovered a potential biomarker that could help develop treatments for multiple myeloma, a rare form of cancer. Currently, multiple…
According to a story from ibdnewstoday.com, a recent study from Italy suggests that people with severe cases of inflammatory bowel disease are more likely to develop non-alcoholic fatty liver disease.…
According to a story from McGill University, researchers from the school, partnered with scientists at the University of Alberta, have unearthed a new discovery that could lead to new therapies…
According to a story from Innovation Toronto, a recent study has helped develop methods that could be used to create cell-based, personalized immunotherapy treatments that could be used to treat…
According to a story from brightsurf.com, a recent research finding suggests that fibrolamellar hepatocellular carcinoma, a rare form of liver cancer that can occur in children, is capable of metastasis…
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