Claire Brinkley Claire Brinkley's daughter Eleanor is diagnosed with progressive familial intrahepatic cholestasis (PFIC) which is a rare disease affecting the liver. As a newborn, she appeared perfectly normal. But at…
CohBar has initiated dosing in their Phase 1b trial of CB4211, which is a treatment for nonalcoholic steatohepatitis (NASH). The biotechnology company focuses on mitochondria based therapies with the goal…
According to a story from BioSpace, the biopharmaceutical company Cerecor Inc., has recently announced that it has restarted operations of its phase 1b clinical trial. This trial is evaluating the…
The Michael J. Foxx Foundation (MJFF) has recently award $8.8 million of grants to various medical professionals for their research on Parkinson's disease. The aim is to develop more treatments,…
According to a story from BioSpace, a case study of a 33 year old man has confirmed that it is possible for humans to get infected with the virus responsible…
According to a story from ScienceBlog, a comprehensive study which focused on children diagnosed with coronavirus/COVID-19 produced some results that surprised scientists and suggested that children could play a greater…
by Lauren Taylor from In The Cloud Copy Huntington’s disease is an inherited disease that slowly causes the breakdown of the nerve cells of the brain, resulting in various disorders…
by Danielle Bradshaw from In The Cloud Copy Perspectum Diagnostics says that they will assess their LiverMultiScan to see if it can serve as a means to find patients that…
by Danielle Bradshaw from In The Cloud Copy It has been found that fingolimod - a drug typically used for multiple sclerosis - may also be effective in treating ANCA-associated…
By Lauren Taylor from In The Cloud Copy Myasthenia gravis is an autoimmune condition characterized by muscle weakness and fatigue of muscles that are under the patient’s voluntary control. This…
Salk Institute scientists have scored a significant gain in their quest to find a functional treatment for type 1 diabetes. According to an article in Salk News, scientists at the…
by Danielle Bradshaw from In The Cloud Copy It’s possible for fat to end up stored inside of the liver due to either obesity, diabetes, certain medications, or high cholesterol.…
by Lauren Taylor from In The Cloud Copy Rheumatoid arthritis (RA) is a chronic inflammatory disorder that affects a patient’s joints, in addition to causing damage to the skin, eyes,…
Gary S. Gilkeson Career Development Award (CDA) The CDA is a grant sponsored by the Lupus Foundation of America that was established to help accelerate research for lupus. The 2020…
If you had told me in March, when the viral pandemic began, that we'd still be staying inside 5 months later, I wouldn't believe you. Yet COVID-19 has become one…
by Caitlin Seida from In The Cloud Copy As if rheumatoid arthritis (RA) weren’t painful enough, those living with the disorder also have to pay extra attention to their hearts…
According to Parkinson's News Today, diet is something that should be monitored in Parkinson's disease patients. Many do not eat enough iron, vitamin B1, zinc, or vitamin D, which was…
Female mammals have XX chromosomes and males have XY. But scientists have never understood how females decide which of their two X's should be active in each of its cells.…
by Lauren Taylor from In The Cloud Copy Myasthenia gravis is a neuromuscular disorder characterized by rapid fatigue and weakness of any muscles that are under the voluntary control of…
Ross Douthat, a writer for the New York Times, was first diagnosed with Lyme disease and a Bartonella infection in 2015 from a deer tick bite. The effects have lingered…
In many cases, autoimmune disorders like myasthenia gravis are treatable. However, there are some cases of refractory (treatment resistant) myasthenia gravis that presents an unmet patient need. However, researchers…
Ascendis Pharma has just announced that their investigative therapy for achondroplasia called TransCon CNP has just received Orphan Drug Designation from the European Commission. This same designation has already been…
by Danielle Bradshaw from In The Cloud Copy Gastroparesis is a condition in which your stomach’s muscles aren’t able to completely move food through your stomach. Symptoms of gastroparesis include…
by Caitlin Seida from In The Cloud Copy Those living with autoimmune disorders like uveitis and multiple sclerosis know all too well that the cells within our bodies meant to…
by Lauren Taylor from In The Cloud Copy Rheumatoid arthritis (RA) is an autoimmune inflammatory disorder that causes inflammation to the lining of your joints while also causing damage to…
Sign Up With a Patient Worthy Account and Share Your Rare Story
- OR -
Make a difference, share your experiences and get paid. Opt-in and join Patient Worthy's panel for paid opportunities such as surveys, market research, patient advisory panels and more.
- OR -
Make a difference, share your experiences and get paid. Opt-in and join Patient Worthy's panel for paid opportunities such as surveys, market research, patient advisory panels and more.
