If you are diagnosed with a serious and rare cancer like acute myeloid leukemia, it is essential that you have access to feedback from leukemia experts. Even if your doctor…
According to a story from PR Newswire, the nonprofit biopharmaceutical company Medicines for Global Health recently announced that the U.S. Food and Drug Administration has approved a drug for the…
According to a story from BioSpace, the biopharmaceutical company AMO Pharma Limited recently announced that the U.S. Food and Drug Administration (FDA) had decided to grant Orphan Drug designation for…
A phase 1/2 study of the drug lumasiran for the treatment of primary hyperoxaluria Type 1 has produced encouraging results, reports Alnylam Pharmaceuticals. The full article can be read here,…
According to a story from coloradocancerblogs.org, a recent study demonstrated that data gathered from PET scans could help providers tailor their treatment more precisely in cases of esophageal cancer, resulting…
Promising data from the ongoing Phase I clinical trial Explorer has been announced by Blueprint Medicines Corporation. The trial is designed to evaluate the effects of the experimental drug avapritinib…
According to a story from pm360online.com, the drug development company ProQR Therapeutics N.V. will be partnering with EB Research Partnership (EBRP) and EB Medical Research Foundation (EBMRF) in order to…
According to a story from businesswire.com, the company Prana Biotechnology Ltd recently announced that it is beginning the recruitment process for its Phase 1 clinical trial of its investigational product…
The U.S. Food and Drug Administration has granted the experimental drug A4250 rare paediatric disease designation for the treatment of progressive familial intrahepatic cholestasis. The full article can be found…
According to Globe Newswire, the United States Food and Drug Administration (US FDA) designated a new orphan drug for the treatment of multiple myeloma on May 9th, 2018. The drug…
Medical Research Network (MRN) is an organisation that specialises in the conduct of clinical trial visits in the patient’s home and supporting clinical trial sites with nursing resources. MRN aims…
There are many mysteries still contained in human biology. Circadian clocks and DNA repair seem to share an interaction that may be one of them. Furthermore, based on research from…
Darwin Ecosystem typically is a name heard in analytic circles. The company specializes in machine-learning and pattern recognition. Now, the company is using their artificial intelligence know-how to help give…
According to a story from the National Institutes of Health, a recent study has revealed that the absence of a specific protein in the cells lining the esophagus could be…
The biotechnology company Bloom Science has found that the ketogenic diet can be an effective treatment for epilepsy due to its effects on gut bacteria. Bloom Science is planning on…
Dicerna Pharmaceuticals has dosed the first patient with primary hyperoxaluria in Group B of a clinical trial of the investigational drug DCR-PHXC. Dicerna has also announced that DCR-PHXC has just…
Why is non-adherence still a problem for many hemophilia patients? There’s a very simple answer here: it’s because hemophilia can be difficult to manage and hard to live with. There’s…
According to a story from Mirror, the advocacy group Patient Concern is calling out the UK's National Health Service (NHS) for failing to treat cancer patients appropriately. The claims are…
According to a story from pm360online.com, the clinical stage corporation Epizyme recently released detailed results from the Phase 2 trial of its leading investigational candidate, tazemetostat. This drug is in…
The Investigational New Drug Application for the experimental drug CTX001 for treating sickle cell disease has been put on clinical hold, announced Vertex Pharmaceuticals Incorporated and CRISPR Therapeutics. This hold…
Pfizer has announced that the medicine Xalkori (crizotinib) has received Breakthrough Therapy designation from the U.S. Food and Drug Administration (FDA) for two potential treatment uses. The full article can be…
According to a story from empr.com, a recent study revealed that gene therapy could allow patients with beta thalessemia to stop having to get regular blood transfusions. The gene therapy…
According to a story from Reuters, the cancer drug developer Loxo Oncology recently released the latest results from the trial testing its investigational therapy LOXO-292. Preliminary results released about a…
The results of a Phase 1 clinical trial of the experimental drug ivosidenib, led by researchers at The University of Texas MD Anderson Cancer Center, have been published in the…
Early trial results in the United Kingdom point to a new vaccine which may extend the lives of cancer patients. The vaccine, designed to help treat glioblastoma, is being described…
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