According to a story from MD Magazine, the FDA has recently approved the first multiple sclerosis treatment catered to children with the disease. In this instance, the agency did not…
According to a story from news-medical.net, researchers working with the Institute for Experimental Pediatric Endocrinology of the Charité - Universitätsmedizin Berlin were able to successfully treat young patients that were obese…
According to a story from azcentral.com, the Trump administration has decided to roll back some budget cuts that put the continued existence of regional Hansen's disease clinics in jeopardy around…
Researchers at Western University and the Lawson Health Research Institute have found that increased water drinking does not slow the decline of kidney function in patients with chronic kidney disease,…
According to a story from The Independent, the 60 years of blood donations from a single man may be directly responsible for saving the lives of 2.4 million babies. The…
New research is showing that patients sometimes use crowdfund websites to pay for fake stem cell transplants and other dubious medical procedures, according to a story from medicalxpress.com. Crowdfunding websites…
The U.S. Food and Drug Administration (FDA) has approved a new use for the treatment Veltassa (patiromer) as an oral suspension (liquid form of the drug) to treat hyperkalemia, a term…
Multiple sclerosis (MS) patients in the United States and other countries around the world are trekking to Russia to undergo a controversial treatment for the neurological disorder that some researchers…
An international team of researchers studying the effects of progressive familial intrahepatic cholestasis (PFIC) in children have found that half of the children had received a liver transplant by age…
In Cincinnati, there are two children, Taryn and King Walker. They are 13 and 11 years old respectively. Taryn and King are excellent students and attend the School for Creative…
A rare but serious disease caused by flesh-eating bacteria has been studied, and researchers have identified the mechanism by which it progresses. This has lead them towards potentially effective treatments…
According to a story from cafepharma.com, Akcea Therapeutics, Inc. recently announced that the FDA's Division of Metabolism and Endocrinology Products Advisory Committee voted to recommend approval of the therapy Waylivra…
According to a story from the Hereford Times, a combination of misdiagnosis and a critical mistake to forgo a simple blood test led to the tragic death of Callum Cartlidge.…
An ongoing study is investigating how water intake could help treat autosomal dominant polycystic kidney disease, says a recent report. Autosomal dominant polycystic kidney disease (ADPKD) is the most common…
A phase 3 Murano clinical trial has shown that combining the drugs Venclexta (venetoclax) and Rituxan (rituximab) could be an effective treatment for chronic lymphocytic leukaemia, reports Cancer Updates, Research,…
Patient Worthy recently attended ALD Life’s Community Weekend 2018, which brought together people and families with Adrenoleukodystrophy (ALD) and Adrenomyeloneuropathy (AMN), and scientists, researchers, and doctors. One of the speakers…
The U.S. Food and Drug Administration (FDA) has just approved a drug called Darzalex (daratumumab) in combination with the drug Velcade (bortezomib), melphalan, and prednisone (known collectively as VMP) for…
According to a story from eurekalert.org, the first patient that received treatment with alipogene tiparovovec reported positive results after an eighteen month treatment period. Alipogene tiparovovec is a gene therapy…
According to a story from Ankylosing Spondylitis News, treatment of chronic pain is always a difficult task for health care professionals. Patients with ankylosing spondylitis (AS) are especially prone to…
According to a story from the Westside Gazette, it is essential for young men to be aware of the risk of testicular cancer and to know when it might be…
According to a story from The Tennessean, mother Melissa Hogan has been inspired by her son Case's Hunter syndrome to start a nonprofit organization called Project Alive. The primary purpose…
No one should outlive their child. Losing two children to the same rare disease is a pain that most parents can never understand and hopefully never will. According to a…
According to a story from Newshub, Freda Evans learned early on that there were no treatments covered under the New Zealand health care system to treat her Pompe disease. Freda…
According to a story from blackpoolgazette.co.uk, the NHS has decided to postpone a decision to approve a drug for the treatment of Batten disease. This illness, which is fatal is…
According to a story from the Yorkshire Evening Post, five-year-old Toby Nye, from Leeds, has been seeing significant benefit from an antibody therapy treatment for his neuroblastoma. The therapy is…
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