As of last Monday, the United States Food and Drug Administration (US FDA) its approval of a new drug to treat thrombocytopenia in cases of chronic liver disease (CLD). Keep…
According to a story from Worldpharmanews, a PARP inhibitor drug that is commonly used to treat ovarian cancer for patients with BRCA gene mutations could also be effective against pancreatic…
In order to keep up with the quick-growing field of gene therapies, the United States Food and Drug Administration (FDA) announced it will provide faster methods of approval for new…
The U.S. Food and Drug Administration has granted Breakthrough Therapy designation to the experimental drug Lenti-D, which is being produced by the gene therapy company Bluebird bio to treat cerebral…
According to a story from news-medical.net, a recent study has revealed that an ingredient commonly found in toothpaste could help patients with cystic fibrosis. The study was conducted by researchers…
According to a story from PR Newswire, the pharmaceutical company BioMarin Pharmaceutical Inc. has recently announced that the U.S. Food and Drug Administration as issued approval for their product pegvaliase-pqpz, which…
The Young family from Oregon, U.S. have used genetic screening to test their embryos for a variation of the BRCA gene that significantly increases the risk of breast cancer, reports…
A new treatment for cystic fibrosis has received a lot of media attention in the UK after the National Health Service (NHS) chose not to fund it due to its…
According to a story from Medical Xpress, the drug adalimumab (marketed as Humira), did not have a noticeable effect on aortic inflammation in patients with psoriatic arthritis or psoriasis. Humira…
According to a story from Business Wire, the gene therapy company Myonexus Therapeutics announced that the U.S. FDA has given Rare Pediatric Disease Designation for its gene therapy candidate MYO-101.…
Researchers at Columbia University have found a way to apply CRISPR, a tool used in gene therapies, to new types of disease, reports News Medical. The study was carried out…
The U.S. Food and Drug Administration (FDA) has awarded Orphan Drug Designation to the experimental drug Sarconeos, developed by the company Biophytis, for the treatment of Duchenne muscular dystrophy. The…
A pre-clinical study of a treatment for Rett syndrome has produced encouraging results, and it is hoped that this will lead to further research. The full story can be read…
According to a story from Medscape, the House of Representatives recently voted to pass a "right to try" bill. The bill they voted on was previously approved by the Senate…
According to a story from CBS Minnesota, legislation was recently filed in Minnesota that could end the practice of step therapy in the state. Step therapy is a common money…
According to a story from globenewswire.com, the drug development company Galectin Therapeutics, Inc., recently announced its plans to go forward with Phase 3 trials for GR-MD-02. The company is dedicated…
It may not be surprising news to find that the United States now pays more for prescription drugs than any other high-income country. This was not always the case however. Read…
The pharmaceutical company Biohaven has announced that they will be using an expanded access program to make an experimental drug for amyotrophic lateral sclerosis (ALS) available to patients before F.D.A.…
A recent study published in the Lancet has investigated the effects of starting chemotherapy on patient survival, according to the UK Government website. It was found that many factors can…
Last week saw the Food and Drug Administration’s (FDA) approval of Aimovig. Aimovig (generically referred to as erenumab-aooe) is a novel approach to treating migraines. It boasts the ability to…
Scientists working at the Broad Institute of MIT and Harvard are trying to build a collection of every drug ever developed. They are planning on using the collection to re-purpose…
According to a story from EPM Magazine, the pharmaceutical company Orchard Therapeutics received Rare Pediatric Disease Designation for its gene therapy drug candidate OTL-200. The therapy is in development for…
According to a story from Financial Buzz, the pharmaceutical company Albireo Pharma recently announced that the first patient has been enrolled in its Phase 3 trial testing its experimental candidate…
A clinical trial that is investigating a drug designed to treat ulcerative colitis has completed patient enrolment, reports Business Wire. Ulcerative colitis is a long-term inflammatory bowel condition. The severity…
The U.S. Food and Drug Administration (FDA) has just approved a subcutaneous version of a drug called Actemra (tocilizumab) for treating patients with active polyarticular juvenile idiopathic arthritis (PJIA) who…
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