According to a story from cbc.ca, Michelle Boich, 33, was facing the prospect of blindness if she is unable to get access to a crucial procedure that could treat her…
According to a story from BBC, Health ministers are starting to put pressure on Vertex Pharmaceuticals to lower the cost of its treatment Orkambi. The drug is indicated for the…
A press release from Aprea Theraputics has just announced the results of a Phase II clinical trial of the drug APR-246 in patients with myelodysplastic syndromes (a group of blood…
According to a story from philly.com, a pair of twins, Marilyn and Sharon Alexander, have dedicated much of their lives to cancer advocacy after a life and death battle nearly…
According to a story from Cosmos Magazine, Dr. Kathryn North is committed to researching the vast expanse of the human genome in order to pinpoint the ways in which genes…
A man in France has been the first person to ever receive two face transplants, reports the BBC. After Jérôme Hamon’s first transplant was rejected he underwent a second transplant…
Doctors told Samantha Youakim she had hepatocellular carcinoma when she was 10 years old. As a result of this rare form of liver cancer, the experts told her she’d only…
Researchers from Newcastle University in the UK have just developed a potentially life-saving device for patients with Addison’s disease, reports Newcastle University. Patients will be given a Quick Response (QR)…
A new clinical study shows how the internet may provide opportunities for therapy. The study’s results detail how an online program called Elevida reduces fatigue in patients with multiple sclerosis.…
The Orthopaedic Institute for Children (OIC) has found that improving the education of patients with hemophilia leads to a large reduction in rates of prosthetic joint infection, reports Bioportfolio.…
A potential treatment for phenylketonuria has progressed to clinical trial stage and the first patient has been dosed, reports Business Wire. This follows successful trials of the drug in non-human…
A biotechnology company called Apitope is developing an innovative new immunotherapy treatment for a range of autoimmune diseases. A press release by the company that can be found here…
Residents think of the Central Florida healthcare system as predictable. It maintains a conservative approach to practices. That was until recently, when the industry invited local video game developers to…
Reviva Pharmaceuticals Inc. (Reviva) announced on April 10th that it received Orphan Drug Designation from the United States Food and Drug Administration (FDA) for one of its experimental candidates. The…
According to a story from The Motley Fool, The gene therapy development company bluebird bio has been working on a treatment for beta thalassemia, and it has the potential to…
According to a story from Financial Buzz, the pharmaceutical company Elsayls Biotech is planning to submit a proposal to the European Medicines Agency (EMA) in order to conduct a clinical…
According to a story from biotechconnectionbay.org, medical researchers are beginning to more closely investigate that possibilities that drug repurposing, or using old drugs for treating different illnesses, could offer. While…
According to a story from statnews.com, a drug derived from substances originating in the cannabis plant may be nearing approval by the U.S. Food and Drug Administration. The drug is…
The pharmaceutical company Lonza has just opened a new state-of-the-art manufacturing facility to produce cell and gene therapies. You can find the full press release here, on Lonza’s website.…
A press release from Applied Genetic Technologies Corporation, which can be found in full at GlobeNewswire, has announced that enrolment for a phase 1/2 clinical study has been completed. The…
A drug called Kineret has been approved by the European Commission in 28 European countries for the treatment of both adult-onset and juvenile-onset Still’s disease, reports Check Orphan. Still’s disease…
According to a story from stv.tv, 14-year-old Kira Noble has been fighting against neuroblastoma for around over four years. She first began to realize that something was wrong when her…
According to a story from wired.com, a new genomics marketplace called Helix will soon start selling genetic tests directly to consumers. These tests are the same ones that doctors use,…
According to a story from globenewswire.com, the pharmaceutical companies Ultragenyx and Kyowa Kirin recently issued an announcement that the U.S. FDA has granted approval to their new treatment Crysvita (burosumab-twza).…
Pfizer has just begun a medical trial for a potential gene therapy treatment for Duchenne muscular dystrophy, and the first patient has been dosed. Click here to read the original…
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