According to a story from Multiple Sclerosis News Today, Dr. Robert Fox and Dr. Robert Bermel, both of the Cleveland Clinic, recently spoke about new treatment improvements that are needed…
Happy Halloween! As the spookiest day of the year approaches, we're highlighting FDA announcements from the last week and a half we think you should hear about. Check them out…
Last time Patient Worthy wrote about Mila Makovec, she was seven and beginning a cutting-edge experimental treatment for her Batten disease. It’s now nine months later, and Mila is showing…
I live in North Carolina. where we were recently hit with a powerful hurricane that caused a lot of damage. Many trees fell on and around my house. One tree…
For some fortunate individuals, cancer is kind of a foreign concept. They obviously know what it is- they hear cancer stories in passing, they may have donated to a charity…
All things Levi. Such a generally fun-loving little boy, yet such a complex bundle of medical conflagrations. All blended and tied up in a robust package that makes Levi a…
According to a story from pm360online.com, the specialty pharmaceutical company Santhera Pharmaceuticals has recently announced of its Phase Ib/IIa clinical trial that will test its experimental product POL6014. This therapy…
According to a story from Inside Philanthropy, a recent case study was conducted in order to determine the main sources of funding for rare disease research. This broad ranging study…
According to a story from technology.org, The National Center for Advancing Translational Sciences (NCATs) has been hard at work coming up with new methods for engaging with the public and…
According to a story from globenewswire.com, Galapagos NV and Gilead Sciences, Inc., recently announced that two clinical trials which were recently published in The Lancet demonstrated that the experimental treatment filgotinib could…
Two children from a Brooklyn family were born with an ultra rare genetic disease called Canavan disease. Their parents' research revealed that gene therapy could possibly treat the disease. Unfortunately,…
Looking back over everything, it all makes sense now. I have been stuck on this never ending roller-coaster for the past 6 years and I have been pushing hard to…
According to a story from EurekAlert!, a Phase I trial is being developed that will test a unique, three part combination treatment for children with neuroblastoma, a rare form of…
According to a story from abc7.com, two surgeons were part of a crowd of thousands that participated in the Los Angeles Cancer Challenge, which took place at UCLA on Sunday,…
According to a story from BioPortfolio, the biopharmaceutical company Deciphera Pharmaceuticals, Inc., recently announced the release of preliminary data from the company's Phase I clinical trial, which is still in…
According to a report by MedCityNews, gene therapies have been catching increasing interest. They’ve been popular in the news and hot talk among medical professionals, but it seems like the…
Multimorbidity, typically defined as having two or more long-term health conditions, has become a topic of increasing focus for healthcare providers. Many elderly people are affected by multimorbidity, with the…
According to a story from pm360online.com, the biopharmaceutical company Ovid Therapeutics recently announced that it had received the 2018 Company Making a Difference Award from the CDKL5 Forum.This recognition was given to…
An ambitious project called the Human Cell Atlas is attempting to study all the cells in the human body – of which there are more than 37 trillion. Researchers hope…
According to a recent press release, patients living with ankylosing spondylitis may soon have another treatment option. The researchers studying the new treatment, known as ixekizumab, recently posted results from…
According to a story from crainsnewyork.com, the biotechnology company Gotham Therapeutics has received financing to the tune of $54 million so that it can begin developing drugs to treat rare…
According to a story from pm360online.com, the biopharmaceutical company Principia Biopharma recently announced that they had achieved $10 million in milestones that are related to the development of its experimental…
I remember being 16 years old and commencing my first drug to help manage my heart rate and endless dizziness. It was strange, because I recall asking my friends if…
According to a story from Medical Xpress, a recent study involving over 400 children has revealed the distinct characteristics of the gut microbiome in ulcerative colitis. Ulcerative colitis is considered…
According to a story from BioSpace, EUSA Pharma and AVEO Oncology recently announced the release of updated interim results from the second Phase of a Phase Ib/2 clinical trial which…
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