We write a lot about rare diseases that affect people but what about the rare diseases among animals? If you own a horse, you've likely heard of Equine Infectious Anemia…
A new device to treat incontinence is being developed by Peter Sayet at Precision Medical Devices Inc., reports the Orlando Sentinel. Incontinence is the term used when people pass urine…
Happy Friday Everybody! This week we're spotlighting two parts of one patient story. We also have news on Alfie Evans and epilepsy research. Sit back and enjoy this week's Editor's…
A Phase 1 clinical trial on patients with cancers that are the result of a change to the tyrosine kinase receptor, also called RET, has produced encouraging results. Cancers caused…
Researchers at the University of Hong Kong have discovered that a drug used to treat muscular dystrophy also works on a hereditary heart disease called Lamin A/C-related dilated cardiomyopathy. The…
A group of researchers led by Professor Gholson Lyon has discovered a genetic mutation that is linked to certain traits, reports Medical Xpress. The method used to discover it was…
According to a story from Neuroscience News, researchers have begun to test the effectiveness of a certain molecule in fighting against childhood brain cancers, such as medulloblastoma. It has the…
A healthy diet and a good exercise regimen go a long way towards maintaining good health. When health care professionals recommend this combination they’re usually trying to keep dangerous diseases…
Richard Kuhns (B.S.Ch.E) boasts twenty years experience working with Morgellons disease and its sufferers. Others consider him to be a leading expert on skin parasites, and the complications of Lyme…
On April 16th, global healthcare company Grifols announced its donation of 25 million international units (IU) of blood clotting factor drugs. These donations occurred within the last year, and are…
I lost my fiancé, Ashley “Bea” Briggs, due to complications from cystic fibrosis a little over a year ago in early 2017. We met early in the summer of 2015…
The prolonged legal battle over Alfie Evans, a toddler with a serious undiagnosed degenerative neurological disease, has reached a final verdict. The UK doctors currently caring for Alfie made the…
The US Food and Drug Administration (FDA) has just approved a new drug called Tavalisse™ to treat adults who have thrombocytopenia as a result of chronic immune thrombocytopenia (ITP), following…
The charity organisation Stand Up To Cancer (SU2C) has just announced that $10 million is going to be given to a team of researchers to fund their work to improve…
According to a story from edinburghnews.com, mother Karen Gray is about to seek access to cannabidiol oil for her five-year-old son, Murray, who has a rare type of epilepsy, Myoclonic Astatic…
According to a story from cbc.ca, Michelle Boich, 33, was facing the prospect of blindness if she is unable to get access to a crucial procedure that could treat her…
According to a story from the US News, Teresa Tostenrud-Hoff, a woman from Kansas, was only 22 years old when she was first diagnosed with primary sclerosing cholangitis. Since then,…
According to a story from BBC, Health ministers are starting to put pressure on Vertex Pharmaceuticals to lower the cost of its treatment Orkambi. The drug is indicated for the…
A press release from Aprea Theraputics has just announced the results of a Phase II clinical trial of the drug APR-246 in patients with myelodysplastic syndromes (a group of blood…
According to a story from philly.com, a pair of twins, Marilyn and Sharon Alexander, have dedicated much of their lives to cancer advocacy after a life and death battle nearly…
According to a story from tapinto.net, the Merrill family was crushed upon learning that their five-year-old daughter Leila was born with Sanfilippo syndrome, a lysosomal storage disease that ultimately causes…
Eva Shea wondered about her daughter. Mimi went to preschool like most children, and seemed otherwise healthy. She had, however, a peculiar, chronic cough. It sounded as though Mimi smoked…
According to a story from Cosmos Magazine, Dr. Kathryn North is committed to researching the vast expanse of the human genome in order to pinpoint the ways in which genes…
Do you have to be tested for an inherited gene mutation if you have already had cancer? Can a woman get a genetic mutation from her father? If you have…
According to a story from the National Center for Advancing Translational Sciences, a group of scientists from the National Institutes of Health (NIH) has unearthed a new mechanism that could…
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