Research into graft-versus-host-disease (GVHD), a condition that can occur after bone marrow transplants, has yielded promising results. A study, reported by BrightSurf, found that a particular group of microRNA molecules involved…
In an effort to better understand patient experiences, researchers at the Massachusetts General Hospital are surveying people with lysosomal storage diseases about how they view their treatments, reports CheckOrphan. The…
Patients with sickle cell disease often face stigma about their need for pain medication because care providers are suspicious of drug abuse, reports The Dallas Post Tribune. Although this is…
Patients with a form of scleroderma called systemic sclerosis are particularly susceptible to developing high blood pressure in their heart and lungs, also known as pulmonary hypertension. A new study…
According to a story from PR Newswire, a recent survey suggests that a greater number of U.S. citizens know about the existence of pancreatic cancer than ever before. This survey…
According to a story from The Telegraph, a team of Chinese and American scientists have used gene editing to create pigs with Huntington's disease. A portion of human genetic material…
According to a story from PR Newswire, the science and tech company Merck recently announced that Mavenclad (cladribine) was recently approved for public use by the UAE Ministry of Health…
A recent study has found that reaching a correct diagnosis can be extremely challenging for people with mitochondrial disease, reports MedicalMalpractise. Patients are likely to have to undergo numerous different…
Now these are the kind of stories we love to read about! Canadian Revée Agyepong is the first adult in Canada to be cured of sickle cell anemia through stem cell…
A proposal by California governor Jerry Brown set its sight on the Discount Drug Program for Medi-Cal patients. A group of healthcare providers, including the Orthopaedic Institute for Children came…
According to a story from scimex.org, a recent data review is calling into question the previously held consensus that common pain medicines such as NSAIDs and paracetamol could make inflammatory…
A new treatment under development has produced promising results in patients with blood cancers and is now being tested in inherited metabolic disorders, reports Financial Buzz. Inherited metabolic disorders are…
Within the last two decades, a type of medicine known as a biologic became popular for the treatment of autoimmune disease such as lupus, or ankylosing spondylitis. The treatments work…
No matter which way you spin it, Ehlers-Danlos syndrome (EDS) is generally not a great time. EDS is a rare genetic condition that affects connective tissue throughout the body. It…
A class of drug called proton pump inhibitors (PPIs) that are used to treat acid reflux and heartburn have been linked to an increased risk of stomach cancer for some…
According to a story from Medical Xpress, a recent study is revealing pronounced differences in the brains of people with fragile x syndrome when compared to the brains of people…
According to a story from ankylosingspondylitisnews.com, a significant proportion of patients stopped taking a biosimilar for infliximab within six months of transitioning to the new medication. This suggests that the…
According to a story from The Irish Times, a new campaign is encouraging people with the rare lung condition idiopathic pulmonary fibrosis to keep exercising. The campaign is centered around…
A drug being developed to treat cystic fibrosis has just been granted Fast Track Designation by the US Food and Drug Administration (FDA), reports PR Newswire. This shows that previous…
According to a story from genengnews.com, the pharmaceutical company Solid Biosciences is pledging to continue developing its investigation drug candidate SGT-001 for Duchenne muscular dystrophy. This is despite its clinical…
Tyler Perry’s Madea may have saved Boone Begner’s life. Born with heterotaxy syndrome, Boone’s heart works with only three chambers instead of four. The condition often becomes extremely dangerous to…
According to a story from wave3.com, time was running out for Leyan Albazzour, who is nine years old. Born in the Palestinian city of Ramallah, the treatment for her Apert…
A recent story from Science Daily is highlighting just how difficult it can be for patients with rare diseases to get an accurate diagnosis. For patients with mitochondrial disease, the…
A new study looking at a test used to diagnose narcolepsy has found that it often produces inconsistent results for the same patients, reports Sleep Review. This highlights a current…
Recent news from Apple shows a new series of emojis coming with the next iOS update. The set intends to “better represent individuals with disabilities.” To accomplish this, Apple partnered…
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