When Kristen Smedley learned her son, Michael, was diagnosed with retinitis pigmentosa, she decided she wouldn't sit back and watch it take away from her son's life, she would take…
It's a fight they didn't choose, but it's a fight they have to face. Individuals diagnosed with sickle cell expressed how much they have to do to get the bare…
According to a story from dailyhealthneeds.com, long term, regular use of protein pump inihibitors (PPI) can majorly increase the risk of contracting stomach cancer. PPIs are commonly used to treat…
The death of a loved one is never easy. It is difficult both to experience and to understand. Mark and Julie Russel lost their son Harry to mitochondrial disease when…
Researchers from Duke Health are hoping to discover new treatments for Lyme disease since the only way to currently manage the disease is by taking consistent antibiotics, which can be…
According to an article from GlobeNewswire, new clinical evidence supports the use of gelpaglutide as a once-weekly treatment for short bowel syndrome. Zealand Pharma completed a Phase I clinical trial…
Rett syndrome might limit 8-year-old Laurel Cooper's ability to speak and do every day tasks, but it doesn't hold back her spunky, sassy attitude, reports University of Wisconsin-Madison News. She will…
15-year-old Jonathan Gutierrez might just be the youngest superhero to date. Recently, a video of him went viral showing how he's sacrificed a lot of his youth to take care…
Originally reported by the Vancouver Sun, children from Langley B.C. are standing up to request access to a potentially life-changing drug as they face the day to day pain onset…
What if we could predict diseases before they happen? What if we could treat diseases like multiple sclerosis and pancreatic cancer before they fully developed. Microsoft is partnering with a…
Physicians at the Canadian Specialist Hospital in Dubai operated on a one-day-old baby with a birth defect called spina bifida, says a recent report. The surgery saved the infant’s life.…
According to an article from FinancialBuzz, the pharmaceutical company Avadel announced that its product FT 218 has been granted orphan drug status by the Food and Drug Administration (FDA) as…
A new fundraising challenge is sweeping all social media platforms once again for amyotrophic lateral sclerosis (ALS), first reported Mom.me. Back in 2014, the ice bucket challenge was a wild success, being…
As an adult living with rare disease, there have been significant gaps in my employment history. I am sure many adults with health complications experience their workforce years this way,…
Researchers from St. Jude Children's Hospital might have just developed a new gene therapy that can build a healthy, functioning immune system for patients suffering from severe combined immunodeficiency, SCID,…
London specialists at the King's College hospital believe they should take an 11-month-old baby Isaiah suffering from multiple diseases off life support to avoid any further pain, reported The Guardian.…
Last month, the pharmaceutical company Sarepta Therapeutics announced the long awaited results of a study that measured lung function in patients with Duchenne muscular dystrophy (DMD) after they took eteplirsen,…
The Australian government has announced that almost that new treatments worth $300 million are being added to the Pharmaceutical Benefits Scheme. This program provides subsidized medical treatments to citizens of…
According to an article from the Chicago Tribune, many medical specialists are coming to the realization that the eligibility criteria for clinical trials should be reassessed. The problem is that…
Minoryx Therapeutics is on their way to making strides for patients with adrenomyeloneuropathy, also known as AMN, reports Labiotech. They just started their phase II initiative to test patients for…
A recent study conducted by researchers from National University of Singapore Medicine laboratory shows that eating vegetables, specifically broccoli, might prevent and even kill cancer cells that develop into colorectal…
A little more hope is given to individuals suffering from Lennox-Gastaut syndrome and Dravet syndrome as GW Pharmaceuticals shared the U.S. FDA will indeed be accepting their application for potential…
Happy Friday Patient Worthians! Believe it or not, we've almost made it through the first month of 2018! This week, we have a story of a young girl with Sanfillipo…
For many - leprosy is nothing but an antiquated disease from biblical times with no present-day relevance. But in fact, nearly 150 to 250 people in the United States and 250,000 around the…
Many cancer and blood specialists will not have encountered systemic mastocytosis. A new drug targets the underlying defect of the disease and will help put doctors on the lookout. Keep…
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