According to a story from Parkinson's News Today, a recent study published in the New England Journal of Medicine highlights the key weakness of Levodopa, one of the most common treatments…
According to a story from statnews.com, the biotechnology company Alexion Pharmaceuticals recently announced that its product Ultomiris, which was recently approved as a treatment for paroxysmal nocturnal hemoglobinuria, was also…
According to a story from the Derby Telegraph, four-year-old Audrina Hatton-Wright was diagnosed with a rare cancer called neuroblastoma about a year ago. This cancer mostly affects children. Doctors initially…
According to a story from Oral Cancer News, a class of immunotherapy drugs called immune checkpoint inhibitors can play a critical role in treating a number of common and rare…
According to a story from the Philly Voice, it has been nearly nine years since Dr. David Fajgenbaum was first diagnosed with idiopathic multicentric Castleman disease. This immune system disorder…
According to a story from Scleroderma News, a recent study found that while treatment approaches for juvenile localized scleroderma were quite consistent in the UK, there were significant disparities in…
According to a story from Science Daily, a team of scientists from the Translational Genomics Research Institute (TGen) have identified the likely cause of a recent outbreak of an unusual…
According to a story from brightsurf.com, a team from the Washington University School of Medicine, based in St. Louis, has succesfully developed a gene therapy that appears to prevent damage…
According to a story from StartUp Health, the organization has recently partnered with Chiesi Farmaceutici, an Italy-based pharmaceutical company, in order to call for innovation and new advancements in the field…
According to a press release from the biopharmaceutical company Cerecor, Inc., the US Food and Drug Administration (FDA) recently agreed to accept the company's Investigational New Drug (IND) application for its…
According to a story from news-medical.net, a team of researchers have found that patients with inflammatory bowel disease display distinct changes to the makeup of bacteria that live in their…
According to a story from PR Newswire, the international drug developer Eli Lilly and Company recently announced the results of a Phase 3 clinical trial testing the company's drug LARTRUVO…
According to a story from Medical Xpress, a recent study found that people who survived Hodgkin lymphoma during their childhood were at a greater risk of developing another type of…
According to a story from BioPortfolio, the biotechnology company Vertex Pharmaceuticals recently announced that the European Commission has approved a label extension for the company's cystic fibrosis drug Orkambi. Under…
According to a story from news-medical.net, a recent study has a found that a hidden disease called hemochromatosis could be a major risk factor for several different joint diseases and…
According to a story from dailymail.co.uk, the story of Cayla Jones is an example of how a serious rare diagnosis can suddenly strike out of nowhere, often from symptoms that…
According to a story from Biotecnika, Penn Medicine & Inovio Pharmaceuticals Inc. have recently announced that the US Food and Drug Administration (FDA) has signaled its approval for the first…
According to a story from dailymail.co.uk, 23 year old Ruby Hill of New Zealand was recently released from the hospital, but it wasn't because she had been successfully treated. It…
According to a story from kios.org, firefighters across the country tend to get cancer, including many rare cancers like mesothelioma, at significantly greater rates than the general population. This is…
According to a story from Fabry Disease News, the drug developer Avrobio recently announced that the US Food and Drug Administration (FDA) has given the company's experimental drug AVR-RD-01 Orphan…
According to a story from bioengineer.org, it has long been known that people with the rare disorder Duchenne muscular dystrophy are at a greater risk of developing a rare cancer…
According to a story from PR Newswire, pancreatic cancer rates in the US are increasing by almost two percent each year. This puts the disease in position to become the…
According to a story from New Scientist, a team of scientists at the Institute of Cancer Research in London were able to develop an AI tool that was able to…
According to a story from BioPortfolio, the Bristol-Myers Squibb Company recently announced that the European Commission has recently approved the first combination treatment for renal cell carcinoma available in the…
According to a story from news-medical.net, a team of researchers from UCLA have successfully developed an approach that allows for the reversal of the mutation that is responsible for the…
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