Rose became acquainted with Patient Worthy after her husband was diagnosed with Acute Myeloid Leukemia (AML) six years ago. During this period of partial remission, Rose researched investigational drugs to be prepared in the event of a relapse. Her husband died February 12, 2021 with a rare and unexplained occurrence of liver cancer possibly unrelated to AML.
Ron Davis and his gene-sequencing technologies were mentioned years ago in The Atlantic alongside Elon Musk (SpaceX) and Jeff Bezos of Amazon fame. Since then, Davis has amassed over…
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The Challenge: He is A Father, A Caregiver and A Scientist Trying to Save his Son and Others With ME/CFS or Chronic Fatigue Syndrome
Calls to Ban CRISPR A scientist named He Jiankui recently shocked the scientific world with his announcement that he had created twin “CRISPR babies”. The babies, a result of…
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CRISPR-Cas9: Scientists and Patients Have Philosophical Differences
It has been nine years since Pfizer acquired the drugs vyndagel and vyndamax. According to a report in Biospace, based on the FDA’s recent approval of the two drugs to treat transthyretin-mediated…
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Transthyretin-Mediated Amyloidosis (ATTR-CM); After Nine Years Pfizer Wins FDA Breakthrough Designation
CRISPR-Cas9, the genome editing tool, has caused quite a stir in the scientific community. According to a recent article in Science Daily, with results published in Nature Communications, CRISPR has…
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CRISPR Uncovers New Gene Fusion as Novel Drug Target for Brain, Ovarian and other Cancers
Newly diagnosed patients may decide to either receive medical treatment or forego treatment based on the results of their diagnostic test. As recently reported in PEW, although it is…
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An In-Depth Discussion About FDA Oversight of Diagnostic Tests and the Effect of Inaccurate Tests on Patients
Although somewhat of an exaggeration, the title of this article falls in line with the thinking of Insitro’s founder, Daphne Koller. In a recent interview with Bloomberg, Koller said that…
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Drug Start Up Founder Says Drugs Will Work For You– But They Don’t Know Why
The Asco Post recently interviewed Dr. Jean Pierre Bizzari, the Executive Vice President of Celgene, a multinational bioparmaceutical company. The interview covered various aspects of research and development (R&D)…
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A Look at Progress in Healthcare and a Glimpse into the Future
Google’s Parent Company (Alphabet) Funds New Gene Editing Company An article recently published in MIT Review reports that Verve Therapeutics announced that it has received funding from Alphabet’s GV venture fund plus…
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Google’s Parent Company (Alphabet) Funds New Gene Editing Company
Google Backs Startup For Treating Heart Disease Via CRISPR Injections May 16, 2019 --Sharing is Caring-- Google Backs Startup For Treating Heart Disease Via CRISPR Injections Once in our life…
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Google Backs Startup For Treating Heart Disease Via CRISPR Injections
An estimated thirty million people in the U.S. are affected by chronic kidney disease. That translates into one out of three adults who are at risk. The majority, however,…
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Investigational Catheter Lock Solution Reduces Infections for Dialysis Patients
China’s attempt to stem the tide of drug addiction through brain surgery has been problematic. Yet a recent article in the Himalayan Times reports that six of the eight…
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At The Crossroads: The Opioid Crisis vs. Brain Implants (A “Pacemaker” for the Brain)
Pharmaceutical companies have spent billions of dollars on Alzheimer’s research. The target has been the toxic protein, amyloid-beta. According to a recent article in NPR News, this theory was…
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ALZHEIMER’S: Scientists are Back to Square One; Will Bryostatin-1 be the Missing Link?
A recent article in the neuroscience section of the Medical Express reports the results of a study conducted by researchers in the Charcot-Marie-Tooth/Hereditary Neuropathy Center at internationally acclaimed Cedars-Sinai.…
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New Research With the Potential to Alleviate Symptoms of Parkinson’s, Alzheimer’s and Charcot-Marie-Tooth Disorders
Three stories of courage are highlighted in Orlando Family Magazine’s annual tribute to the medical community. The first example relates to a mother, Eva, for her courage in opting…
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Three Inspiring Stories of Courage
It has been less than two years since Cytokinetics’ previous ALS muscle drug, tirasemtiv, failed to meet its endpoint in a Phase III trial to treat ALS. (That was after…
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A Biotech Company Finds a Silver Lining After Clinical Trial Results Show Failure of its New ALS Drug
A recent article in CBC News describes the heartbreak and struggle of a Canadian couple appealing to the Canadian government to fund medication for their younger son. Both their children, Andre…
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Parents are Worried That Only One of Their Two Children Will Get Access to Cystic Fibrosis Drug
An article in Globe Newswire quotes National Institute of Health statistics for malaria as being between 300 to 500 million cases worldwide resulting in 1.5 to 2.7 million deaths annually. People living…
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MALARIA: Between One Million and Two Million Deaths Each Year Worldwide. This Company is on Target to Treat Severe Malaria
A recent report that was published in the Swiss Medical Weekly outlines data gathered by a Swiss panel of experts on plasma cell myeloma. The report offers an update and…
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New Data on the Difference Between Plasma Cell Myeloma and Smoldering Myeloma Has Treatment Implications
The News Hub at Washington State University recently carried an article describing initial success by researchers towards developing a drug for a rare form of muscular dystrophy. Several thousand people…
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Researchers Believe Lithium May be Key to Developing a Drug for Limb Girdle Muscular Dystrophy
Researcher: “MND is not an incurable disease. It is an underfunded disease” The Trinity Times recently interviewed Prof. Orla Hardiman on the subject of motor neuron disease (MND), also…
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Researcher: “MND is Not an Incurable disease. It is an Underfunded Disease”
A recent posting by the Leukemia and Lymphoma Society references the Beat AML Master Trial. The trial evaluates targeted therapies to treat acute myeloid leukemia (AML) and was launched…
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The LLS Ground-Breaking Precision Medicine Approach Master Trial BEAT AML Releases Third Year Test Results
In about five years India’s population will exceed that of China which is currently ranked number one according to population. Contrast these numbers with the fact that only ten percent…
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Rare Diseases: Only 10% of India’s 1.37 Billion People Have Health Insurance
Dr. David Porteous, a General Practitioner in Bristol, England recently reported to the Bristol Cable, a community-run newspaper, that he does not agree with the extensive list of treatments being…
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GPs and Specialists in UK are Challenging the Restrictions That Deny Patients Access to Treatment
Ash Clinical News recently interviewed Dr. Bruce Leff of Johns Hopkins in connection with “hospital-at-home”, one of the major changes occurring in hospital care. Dr. Leff and his team at…
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In-Patient Hospitalization vs. At-Home Programs: Will Doctors Be Making House Calls Again?
According to an article in Biospace, the FDA is currently reviewing data from the Phase III STRIVE clinical trial for possible approval of Zolgensma as gene therapy for spinal…
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New Drug Under Review by the FDA to Treat the Most Lethal Form of Spinal Muscular Atrophy