Researchers Find Gut Bacteria that Can Change Type A Blood to Type O
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Researchers Find Gut Bacteria that Can Change Type A Blood to Type O

Blood Donations For many people living with a rare disease such as Beta thalassemia, Hemophilia, Aplastic Anemia, Myelodysplastic syndromes, Acute Promyelocytic leukemia, and others, blood transfusions are not uncommon. For…

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Norah Needs You: Help This Young Girl Find a Bone Marrow Donor 
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Norah Needs You: Help This Young Girl Find a Bone Marrow Donor 

At four years old, Norah Gratz-Lazarus of California is a sweet, bubbly girl, full of spirit. She's a big sister, and loves jokes, ice cream, and chocolate chip cookies. However, Norah…

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Finally Severe Aplastic Anemia Patients will Have Access to Eltrombopag
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Finally Severe Aplastic Anemia Patients will Have Access to Eltrombopag

Eltrombopag (Promacta) has now been approved for all individuals in the US with severe aplastic anemia. The drug will be accessible to both pediatric and adult patients. This is huge news.…

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Aplastic Anemia and MDS International Foundation: 2018 Scientific Symposium
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Aplastic Anemia and MDS International Foundation: 2018 Scientific Symposium

At the 2018 Aplastic Anemia and MDS International Foundation’s (AAMDSIF) International Bone Marrow Failure Disease Scientific Symposium of March 2018, Dr. David Margolis from the Medical College of Wisconsin, and…

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Welcome AAMDS, a New Patient Worthy Advocacy Partner!

We're happy to introduce a new partner to Patient Worthy's mission of advocating for rare disease patients! The Aplastic Anemia and MDS International Foundation (AAMDS) supports, connects and educates patients, caregivers…

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FDA Gives Priority Review to Promising Treatment for Severe Aplastic Anemia
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FDA Gives Priority Review to Promising Treatment for Severe Aplastic Anemia

According to a story from pm360online.com, the U.S. Food and Drug Administration (FDA), has given Priority Review status to eltrombopag (marketed as Promacta) after impressive clinical trial results. Eltrombopag was…

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Donate Blood in the Name of Bleeding Disorders Awareness Month
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Donate Blood in the Name of Bleeding Disorders Awareness Month

Let's talk blood donation. I recently spoke with a man from a small African country who suffers from hemophilia. He told me that when he was growing up, there was no…

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Aplastic Anemia: This Fabulous Fairy Princess Will Warm Your Heart
Dreams are coming true for this little girl living with aplastic anemia! Source: www.pixabay.com

Aplastic Anemia: This Fabulous Fairy Princess Will Warm Your Heart

I feel like shouting from the rooftop after reading about this 7-year-old girl named Yasmin. After a long hospitalization that spanned several months, she finally got released because her body…

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