Hereditary angioedema (HAE) is a rare condition which causes severe swelling in various areas of the body. Takhzyro has been approved as a treatment for this disease. The drug was created…
According to a story from the Tenterfield Star, a fundraiser was recently held for Tommy Johnston, a one year old boy who was diagnosed with the rare Niemann-Pick disease type…
February 2nd is Neuroblastoma Awareness Day! It's important to know more about this rare cancer, since knowledge and familiarity are often the engines of progress. What is Neuroblastoma? Neuroblastoma is a…
According to a publication from PR Newswire, CloudMedx, a technology company from Palo Alto, is touting impressive results following a simulated exam pitting human doctors against their "deep learning" Clinical…
Rare disease families deal with a lot. The last thing they should be forced to have on their mind is how to get access to care. Unfortunately, for many parents…
According to a story from BBC, it is becoming increasingly clear that a lot of the common phrasing and language that we use to talk about cancer and cancer patients…
Sickle cell disease (SCD) is a rare blood condition. It causes sickling in the red blood cells which results in the blockage of blood vessels and capillaries. The sickling process…
Non-tuberculous mycobacterial (NTM) infections are caused by bacteria found in the environment. In healthy individuals, these bacteria normally cause no harm. However, for those who have a compromised immune system or who…
Happy Wednesday! While it's felt like January was going to last forever, we're almost through the first month of 2019. As we gear up for February, we want to reflect…
A rarely addressed subject that comes up in discussions about people with disabilities is the subject of romantic relationships, intimacy, and parenting. More than likely, a lot of day to…
According to a story from sectorpublishingintelligence.co.uk, the biopharmaceutical company Processa Pharmaceuticals, Inc. recently announced that the first patient had been dosed in the company's Phase 2 clinical trial. This trial…
According to a story from pm360online.com, the drug developer Innate Pharma SA recently announced that its experimental therapy IPH4102 has been granted Fast Track designation from the US Food and…
According to a story from wired.com, everything changed for Sonia Vallabh and her husband Eric Minikel after Sonia's mother died from a mysterious illness. Sonia's mother Kamni was in her…
In an article published by SciTech Europa, Professor Susanne Gerit Kircher with the Medical University of Vienna discusses some of the difficulties experienced by professionals on the front lines of rare…
Notable Labs Notable Labs was created after founder, Matt De Silva, felt he was left in a helpless point, following a year of research on treatment options for his father's Glioblastoma…
According to a story from statnews.com, the biotechnology company Alexion Pharmaceuticals recently announced that its product Ultomiris, which was recently approved as a treatment for paroxysmal nocturnal hemoglobinuria, was also…
An article recently published by the Washington Post is highlighting a few of the risks associated with fertility treatments that some doctors feel are de-emphasized by existing medical literature. What…
According to a publication from the Stamford Advocate, the Connecticut-based Alliance for Cancer Gene Therapy (or ACGT) has welcomed a new president and CEO in Kevin Honeycutt. Honeycutt has announced…
The History of West Nile Virus The West Nile Virus (WNV) was named for the location where it was originally found- the West Nile district in Uganda. It was discovered…
The most common treatment for someone who is discovered to have early stage kidney cancer is surgery. The patient's tumors and a part of their kidneys are removed through a…
According to a story from the Derby Telegraph, four-year-old Audrina Hatton-Wright was diagnosed with a rare cancer called neuroblastoma about a year ago. This cancer mostly affects children. Doctors initially…
According to a story from Oral Cancer News, a class of immunotherapy drugs called immune checkpoint inhibitors can play a critical role in treating a number of common and rare…
According to a story from the Philly Voice, it has been nearly nine years since Dr. David Fajgenbaum was first diagnosed with idiopathic multicentric Castleman disease. This immune system disorder…
According to a story from Physician's Weekly, the pharmaceutical company AbbVie, Inc. recently announced that its cancer drug Imbruvica failed to measure up in a recent clinical trial in which…
According to a story from Science Daily, a team of scientists from the Translational Genomics Research Institute (TGen) have identified the likely cause of a recent outbreak of an unusual…
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