Days in 2018, we have some great statistics on 2017! According to the United Network for Organ Sharing (UNOS), over 10,000 organ donations were made, marking the first year that number has been…
Deciphera Pharmaceuticals recently announced the initiation of a Phase 3 clinical study. The study aims to investigate the safety and effectiveness of a new drug targeting gastrointestinal stromal tumors. Keep…
The Loma Linda University Eye Institute in California performed its first-ever procedure using a FDA-approved procedure, which can deter the effects of keratoconus - a rare progressive disease of the cornea,…
According to a story from financialbuzz.com, the pharmaceutical company MabVax Therapeutics just announced initial dosing for patients and the completion of enrollment for its Phase I trial study. The study…
America first started noticing South African runner Annie Bothma at the Roy Griak invitational in 2015. She came in third! Not only is she talented, but her preferred running technique…
According an article from CityNews Toronto, an anti-psychotic medication is undergoing clinical trials in the treating of amyotrophic lateral sclerosis. In other studies, the treatment has shown to help slow…
Did you know estrogen can help protect the body from multiple sclerosis? A recent study by a team at UCLA solidified this finding and discovered how it works. Read on…
According to a story from wepclinical.com, the Creating and Restoring Equal Access to Equivalent Samples Act, also known as the CREATES Act, was introduced in 2017 in order to accelerate…
On January 5th the NFL announced it will be contributing just over $16 million to research. The money will be split among three different programs that focus on neurodegenerative diseases.…
As a wave of female empowerment cascades our nation - like the Time's Up and #MeToo movements - let's also turn our attention to Cervical Health Awareness Month. Cervical Health…
Midatech Pharma just received verbal confirmation from Polish regulators to conduct the first European in-human study for a treatment that could potential aid those with carcinoid cancer and acromegaly, reported…
According to a story from Syosset Jericho Tribune, the charity basketball fundraiser called Hoops for Harrison is back again this year. The tournament was named after Harrison Gillman, who now…
Although it never should have happened, at least the right course of action was taken! Reggie Bibbs of Houston, Texas was turned away from his Uber driver when he requested…
REGENXBIO announced last month that the Investigational New Drug application (IND) is active for a Phase I/II clinical trial of RGX-121 for the treatment of Mucopolysaccharidosis Type II (MPS II)…
At only six years old, Simeon Augustus Peterson, also referred to as "Mr. Pete," was diagnosed with Hansen's disease. From then on, he lived the rest of his life cut…
January 5th was not only a great day for the Butler basketball community, it was a dream come true for the bulldog fan Seth Dennison, reported Fox 59. The 7-year-old…
According to a story at medpagetoday.com, a recent study showed that stem cell transplant could be a viable new method for treating scleroderma, and could be more effective than previous…
RespireRx Pharmaceuticals announced last month it was cleared to resume its ampakine CX717 clinical trials to evaluate the drug’s efficacy in several central nervous system and respiratory disorders, including Pompe…
Last month, the FDA has granted Achillion Pharmaceuticals orphan drug designation to ACH-4471 for the treatment of patients with C3 Glomerulopathy (C3G). According to the FDA, the Orphan Drug Designation program provides…
New research is helping experts understand the underlying causes of idiopathic pulmonary fibrosis on the molecular scale. When solving any problem, disease included, it is best to start by understanding…
Nothing is worse for a family than hearing the word “cancer,” especially when it involves a child. The Tyson family was ready to start their perfect life eleven years ago.…
According to a story from the National Hemophilia Foundation, the Swedish pharmaceutical company Orphan Biovitrum announced that its first patient was registered for a new phase 4 clinical trial. The…
Another successful partnership in the rare disease community has come to fruition, reports The Pharma Letter. Just this past week, CureVac and Arcturus Therapeutics will become a powerhouse together with…
Happy Friday, Patient Worthians! This week we have articles about people working together on different types of rare disease teams. We have stories from a family who supports two children…
Patient Worthy is proud to announce we are participating in Patients as Partners EU in London, UK on January 23rd. Patients as Partners EU represents the only conference opportunity in Europe…
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