According to a story from globenewswire.com, the biopharmaceutical company Apellis Pharmaceuticals, Inc. has announced that it is currently making plans to submit a New Drug Application (NDA) to the US…
According to a story from UNC Health Care, the Belgian drug company Argenx recently announced that its investigational treatment efgartigimod has performed well in a phase 3 clinical trial. The…
Many myasthenia gravis patients do not benefit from already existing therapies, such as steroids, acetylcholinesterase inhibitors, or immunosuppressants. It is this fact that has pushed many biotechnology companies to start…
Daily use of Nuplazid (pimavanserin) leads to strong and sustained reductions in the frequency and severity of hallucinations and delusions in people with Parkinson’s disease psychosis, according to data from…
In a recent article that appeared in Science Magazine, Amy Boland described her twelve-year quest to find a cure for the cancer that invaded her lymph system. At first,…
Immune-Onc Therapeutics recently received clearance from the FDA to begin trials of IO-202, a treatment for acute myeloid leukemia (AML). This news comes after the cancer immunotherapy company filed an…
From 1985 to 1990, Michael J. Fox entertained the world with his portrayals of Marty McFly in the Back to the Future series. Although Marty is figuring out time travel as he…
Finding out that you are pregnant conjures up a lot of feelings: nervousness, excitement, happiness, and love. But if you have a rare disease or disorder, especially a genetic condition,…
Medical professionals are already aware that inhaling air pollution can increase one's risk of a number of conditions, including respiratory and heart diseases. They are now discovering that it can…
Medical cannabis has been touted as an effective treatment for a variety of conditions: glaucoma, epilepsy, multiple sclerosis, and even cancer. But is this controversial product also a potentially treatment…
If you think about it, our brains are pretty amazing. It is one of our most complex features and contains tens of billions of neurons which help control the…
In high school, Chuck Graham loved sports. He was a student-athlete dedicated to his teams. But then, at 16 years old, a car accident paralyzed Graham from the chest…
Dr. Changcheng Zheng of the University of Science, China, recently spoke to Cancer Network about a case study indicating that tocilizumab (Actemra) could effectively treat people with multiple myeloma…
What's better than a good night's sleep? In my opinion, waking up feeling refreshed is one of the nicest feelings. But for patients with Parkinson's disease, it can be difficult…
Scientists at the Tohoku University reported in Asia Research News that antibodies are responsible for the difference between various disorders and multiple sclerosis (MS). These disorders affect the myelin sheath…
What would motivate a man, who has been living with amyotrophic lateral sclerosis (ALS) for twenty years, to accept an invitation to become part of a five-man team and…
The events of the past week-- and the past few hundred years-- have brought up a lot of sadness, anger, and reckoning in our country. There are so many ways…
A seemingly healthy baby was born in China. But as she grew up, her family started noticing that their daughter wasn't hitting motor milestones. She didn't start walking until she…
Recently, researchers from European Molecular Biology Laboratory (EMBL) looked to understand the cause of pulmonary arterial hypertension (PAH). They collaborated with Stanford University through the Life Sciences Alliance. Because…
In an article in Medical Xpress, Japanese doctors have performed a “first” by transplanting liver cells (made with embryonic stem cells) into a newborn. The six-day-old infant was diagnosed with…
As reported in Guru Focus, biotech company Protagonist Therapeutics has announced progression in their Phase 2 study on PTG-300 as treatment for patients with polycythemia vera, a rare cancer. Dr.…
According to a story from prnewswire.com, the Chiesi Global Rare Diseases and the biopharmaceutical company ProTalix Biotherapeutics have recently announced that they have submitted a Biologics License Application (BLA) for…
By Danielle Bradshaw from In The Cloud Copy The cells of hemophilia A patients were taken and genetically modified so that they would create an active clotting factor VIII (or…
IBDsmart Researchers at the University of Otago, led by Michael Shultz, have developed a new app called IBDsmart to help patients with ulcerative colitis or Crohn's disease receive care remotely.…
According to a story from Pulmonology Advisor, a recent study has evaluated risk factors for the appearance of bronchiectasis in patients with aspirin-exacerbated respiratory disease (AERD). A small number of…
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