Uncertain times may be the understatement of the year so far. When the news of COVID-19 (coronavirus) caught our attention, there were a lot of people frozen in disbelief and…
As reported in CCAKids Blog, 2020's contagion has imposed a strange new set of rules and precautions for leaving the house. The latest CDC recommendation has told all of America…
According to CNBC, there is a shortage across the country of a very important medication: hydroxychloroquine. This is somewhat unsurprising. After all, the Trump administration has been vocal about the…
According to Business Insider, cases of COVID-19 and deaths attributed to it are rising rapidly. The pandemic was officially declared on March 10th, just about one month ago. At the…
Seneca Biopharma, Germantown, Md., issued a press release announcing its recent meeting with the FDA to discuss elements of a final design and protocol for a Phase 3 trial investigating…
According to a story from Porphyria News, Lucia Monaco, PhD, is the chair of the International Rare Diseases Research Consortium (IRDiRC). Despite the ongoing disruptions caused by the coronavirus/COVID-19 pandemic,…
According to a story from Spectrum News, the Andrews family has been dealing with a rare disease called Niemann-Pick disease type C for years. Parents Pam and Chris knew early…
According to an article in The Asahi Shimbun, Japanese scientists have developed a new vaccine to mitigate neuronal degeneration caused by Alzheimer's disease. The vaccine, delivered nasally, had promising results…
Hi everyone, We hope everyone's doing okay-- whatever that means for you right now. Today we have an article about how rationing systems during COVID-19 pandemic is affecting people who…
According to a report by ABC News, Virtua Health, one of the largest healthcare providers in New Jersey, claimed to have a forty-year history of organ transplant completions. Nonetheless, a…
According to an article in Science Daily, Professor David Nicewicz and a team of researchers at the UNC Department of Chemistry, discovered a method of creating tracers used in…
According to Oren Goldshtein, CEO of Vectorious Medical Technologies, remote patient monitoring is needed now more important than ever. Nobody knows how long the COVID-19 pandemic will last or…
A person with diabetes is not able to properly make or use insulin well. Advancements in science are now seriously looking at updating and perfecting ways to help people…
A press release from the US Food and Drug Administration (FDA) recently announced the approval of the drug selumetinib (marketed as Koselugo) for the treatment of patients aged two years…
NICHD The NICHD is the The Eunice Kennedy Shriver National Institute of Child Health and Human Development, one of the National Institutes of Health (NIH). It is the center for…
According to a story from XTalks, pulling off a clinical trial testing a new drug in a scientifically rigorous manner is no simple feat. It requires the triangulation of a…
According to a press release from the Mayo Clinic, new research findings show that in-utero neurological surgery for patients with spina bifida is more successful in strengthening brain structure…
During the past fifteen years there has been ever-increasing interest in scientific research in the role of microbiome in human health. According to a recent article in Forbes India, this…
A two-part series of “The Gene”, a PBS documentary, will air on April 14, 2020. The film, by Ken Burns, is based on a book with the same title written…
If you're worried or anxious because of COVID-19, you're not alone. If wondering about the intersection of rare diseases and COVID-19 only increases that anxiety, well, we're with you…
According to a story from Wexford People, 8-year-old Mia-Lily Ruttle wants to spread some hope to people around the globe. The girl, who has neurofibromatosis, was upset by the impact…
Judy had been living an active lifestyle after she retired as a library assistant for Portland Public Schools for 30 years. She kept up with her lifelong love, ice skating,…
Crohn's disease is a very rare condition in Taiwan, as only .2 of every 100,000 people are diagnosed with it. Because of this rarity, there is little to no awareness…
According to a story from globenewswire.com, the biopharmaceutical company Liquidia Technologies, Inc. just announced that the company's New Drug Application (NDA) has been officially accepted by the US Food and…
According to a recent article in Parkinson’s News Today, the drug prasinezumab has entered the second half of a Phase 2 trial. An earlier trial, NCT02157714, showed that the therapy…
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