According to a story from the Sydney Morning Herald, two-year-old William McLennan, son of Naomi Taylor and Ben McLennan, was diagnosed with spinal muscular atrophy about a year ago. The…
The UK government is being petitioned to hold a referendum on the decriminalisation of the drug cannabis. This has implications for people with diseases that may be helped by using…
According to a story from philly.com, a recently released set of guidelines is placing new emphasis in the need for patients not to delay treatment during the early stages of…
Phillippa Farrant, whose son, Daniel, has been diagnosed with Duchenne muscular dystrophy (DMD), recently appeared in Parliament in the UK to fight for improved access to care and treatment for…
According to a story from Harvard Health Publishing, a common problem with the upper chambers of the heart which cause the heart to pump inefficiently may be made less severe…
Doctors haven’t been able to work out the cause of a young woman’s medical symptoms, and now the New York Times is appealing to the public for suggestions. This article…
A gene therapy being developed as a treatment for Sanfilippo syndrome has just been awarded Regenerative Medicine Advanced Therapy (RMAT) status in the US, reports GlobalGenes. Sanfilippo syndrome is a…
According to a story from PR Newswire, The Marfan Foundation and Backpack Health are partnering so that the foundation can begin the creation of a patient registry for people affected…
The Australian government will subsidize a new treatment for Hodgkin lymphoma, bringing its price down from $200,000 per course to $39.50 for most people, and $6.40 for concession patients, reports…
According to a story from biotechprism.com, ten-year-old boy Jed Kagan of South Africa was crippled by debilitating pain when he first appeared at the Red Cross War Memorial Children's Hospital in…
When people are faced with cancer, their main concerns are understandably treatment and survival. However, many are shocked to discover that when they survive cancer, another sinister blow on their…
The US Food and Drug Administration (FDA) has just approved the drug Vonvendi for use in adult patients with von Willebrand disease who are undergoing surgery. This is an extension…
Imagine not being able to eat because you cannot swallow your food. Add to that intolerable pain and the inability to sleep at night. These are some of the symptoms…
In order to honor Cystinosis Awareness Day, which takes place on May 7th each year, a man will attempt to walk 57 miles in a single day in order to…
Happy Friday Everybody! This week we're spotlighting two parts of one patient story. We also have news on Alfie Evans and epilepsy research. Sit back and enjoy this week's Editor's…
A healthy diet and a good exercise regimen go a long way towards maintaining good health. When health care professionals recommend this combination they’re usually trying to keep dangerous diseases…
Richard Kuhns (B.S.Ch.E) boasts twenty years experience working with Morgellons disease and its sufferers. Others consider him to be a leading expert on skin parasites, and the complications of Lyme…
On April 16th, global healthcare company Grifols announced its donation of 25 million international units (IU) of blood clotting factor drugs. These donations occurred within the last year, and are…
The prolonged legal battle over Alfie Evans, a toddler with a serious undiagnosed degenerative neurological disease, has reached a final verdict. The UK doctors currently caring for Alfie made the…
According to a story from BBC, Health ministers are starting to put pressure on Vertex Pharmaceuticals to lower the cost of its treatment Orkambi. The drug is indicated for the…
According to a story from philly.com, a pair of twins, Marilyn and Sharon Alexander, have dedicated much of their lives to cancer advocacy after a life and death battle nearly…
A team of childhood cancer researchers, known as the Pediatric Cancer Dream Team, were first created in 2013 through collaboration between the charitable organizations Stand Up To Cancer (SU2C)…
So what is Fabry disease you ask? You came to the right place! Fabry disease is a genetic, lysosomal storage disorder that occurs when a specific kind of fat known…
The US Food and Drug Administration have just approved a genetically engineered swine research model for the rare disease ataxia telangiectasia for commercial use. The model, officially named the ExeGen…
Residents think of the Central Florida healthcare system as predictable. It maintains a conservative approach to practices. That was until recently, when the industry invited local video game developers to…
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