Diseases affecting the brain are often pose numerous difficulties in research. One such challenge is that animal models of the diseases never quite replicate the human reality. In mice, for…
Gastroschisis Study Cincinnati Children’s Medical Center, Texas Children’s Hospital, and Avery’s Angels are working together to try to learn more about the long-term gastrointestinal issues that people born with gastroschisis…
According to a recent article for myscience.org, there is new potential for genetic therapy to cure the often deadly neurodegenerative disorder known as Gaucher disease. The new studies were first…
According to a report by Science Daily, researchers recently discovered a disease in monkeys which imitates human Batten disease. Establishing the closest analog to the condition in humans, the version…
According to a Science Daily report, new research by a group in Liverpool recently uncovered a drug for the treatment of alkaptonuria. Researchers published the collaborative study in the journal…
According to a story from the pharmaceutical company Takeda, the company recently released the results from its clinical trial testing an experimental subcutaneous formula of the drug vedolizumab. The drug…
A Phase 1/2 clinical trial of the experimental drug NV1205 in patients with childhood cerebral adrenoleukodystrophy (CCALD) has been initiated, announced NeuroVia Inc. The source article can be found here,…
According to a story from Beyond the Dish, a new experimental treatment for spinocerebellar ataxia was given the go-ahead from the U.S. Food and Drug Administration for testing. The investigational…
According to a story from BioPortfolio, the company Mologic Ltd recently announced that its clinical trial to test HeadsUp, its urine-based diagnostic tool, is starting. The clinical trial will specifically…
According to a source article that can be found here on Ultragenyx’s website, the first patient has been dosed in a trial of an investigational gene therapy called DTX401 that…
A study is planned to investigate the effects of the experimental drug PTC596 in children with recently diagnosed diffuse intrinsic pontine glioma and high-grade glioma. The study is made up…
The first patient has been treated in the Empowers study, a clinical trial investigating an experimental gene editing therapy for the treatment of mucopolysaccharidosis type I. The source article, which…
According to a story from Buffalo News, Brett Perla was graduating high school when he first starting to experience symptoms of a rare condition of the cornea called keratoconus. This…
According to PRNewswire, Beverly Hills and Frankfurt based INFUSIO donated $5,000 each of their patient’s Lyme disease treatment in May. Interest in the program was high. As a result, INFUSIO…
According to University of Wisconsin News, UW-Madison professor David Beebe and his colleague Anna Huttenlocher, fellow UW professor, were awarded a $3.7 million grant from the National Institutes of Health (NIH)…
According to Business Wire, a pharmaceutical company, Aurinia Pharmaceuticals Inc., recently announced that they have enrolled the first lupus nephritis patients in the AURORA 2 extension study. Not only this, but Aurinia…
According to a report by The Herald Scotland Online, a landmark study recently reveled flight crew to be exposed to greater than average risk of thyroid cancer. Surprisingly, the results…
According to a report by Evening Times, two new drugs targeting Huntington’s disease are on the way. Developed by Wave Life Sciences, the new drugs will soon undergo clinical trials…
Who couldn’t use a little extra money now and again? Better still, what if earning that money was as easy as a mouth swab? According to a report on Journal…
According to a story from WebMD, a recent study concludes that the rates of diagnosis for thyroid cancer have been steadily increasing recently, and that it is over treated in…
According to a story from HSC News, Dr. Peter Kuhn from the University of South Carolina (USC) is developing a navigational tool that aims to personalize treatment based on a…
According to a story from pcmag.com, the pharmaceutical company GlaxoSmithKline (GSK) has recently partnered with 23andMe as part of a four year long agreement that will grant the company exclusive…
Pancreatic cancer is known to be dangerous because of its ability to spread. The most common areas the cancer will metastasize are the liver and lungs. In many cases, the…
Treatments for neurological diseases have been developing rapidly in the modern era. Despite the development of new medicines and therapeutic techniques for many conditions, no cure has been found for…
According to a story from rdmag.com, researchers from the University of Toronto have discovered a critical mechanism that helps facilitate the normal DNA repair process. This mechanism could have implications…
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