Researchers have uncovered a new way to treat cancer that could lessen the side effects that patients often experience from chemotherapy. At the same time, it improves the curative power…
Pulmonary fibrosis is a condition that is caused by scarring of the lungs which can lead to shortness of breath and other respiratory issues. Some cases of COVID-19 have lead to…
Complex Regional Pain Syndrome Complex regional pain syndrome (CRPS) is a rare condition that causes prolonged pain after a minor injury. This pain is severe and can be debilitating. One…
The FDA has recently approved of GlaxoSmithKline's (GSK) treatment for lupus nephritis (LN), BENLYSTA. This therapy is the first of its kind, meant to treat systemic lupus and adults with…
Albireo has recently initiated their Phase 3 ASSERT trial, according to GlobeNewswire. This study will evaluate odevixibat as a treatment for Alagille syndrome. This therapy fits well with Albireo's mission,…
Before 1983, there were few treatments for rare diseases. Various obstacles stood in the way, including little representation for patients, few incentives, and a lack of resources. Fortunately, the Orphan…
With the overall focus of the Reuters Pharma & Patient USA 2020 conference being the relationship between patients and drug manufacturers, a key topic focused on how companies can form…
According to a story from BioNews, a recent study has revealed more information about the maternal protein SMCHD1, and impacts to the normal function of this protein could play a…
According to a case study published in Hindawi, a case study of a 36 year old Black woman provided an unusual and rare example of intestinal pseudo-obstruction presenting as the…
According to an article from Cancer Therapy Advisor, medical professionals have created a new, simplified prognostic score for patients affected by myelodysplastic syndromes (MDS). This score utilizes multiparametric flow cytometry…
by Lauren Taylor from In The Cloud Copy Spinal muscular atrophy or SMA is a disease that occurs due to loss of motor neurons, which are the nerve cells that…
by Lauren Taylor from In The Cloud Copy Sickle cell disease or SCD is a type of red blood cell disorder in which the normally round red blood cells are…
Visual hallucinations have been a known symptom of Parkinson's disease for a long time, but the cause has evaded medical professionals. That is, until now. A recent study, titled "Visual…
by Danielle Bradshaw from In The Cloud Copy The National Institutes of Health is funding a study throughout the entire United States with the goal of figuring out what causes…
by Danielle Bradshaw from In The Cloud Copy Research that has recently been made available reveals that lupus nephritis - a kind of kidney disease that’s related to lupus -…
by Lauren Taylor from In The Cloud Copy Myalgic encephalomyelitis/chronic fatigue syndrome (ME/CFS) is a debilitating condition in which the affected patient has overwhelming fatigue that does not improve even…
The Reuters Pharma & Patient USA 2020 virtual conference included a number of shorter presentations that focused on specific approaches to help drug companies better meet the needs of patients.…
by Lauren Taylor from In The Cloud Copy Myalgic encephalomyelitis/chronic fatigue syndrome (ME/CFS) is a complicated and debilitating condition in which affected individuals are unable to perform their daily activities…
Kura Oncology, a San Diego biopharmaceutical company, was recently featured in a Globe Newswire article, announcing its first-in-human dose escalation of KO-539 being evaluated in the Komet-001 trial (NCT04067336). The…
by Lauren Taylor from In The Cloud Copy A variance in the amount or makeup of the bacteria in a person’s gut, called dysbiosis, could have strong implications for the…
According to a story from SMA News Today, a recent case study has reported instances in two spinal muscular atrophy (SMA) patients in which repeated administrations of the therapy nusinersen…
by Lauren Taylor from In The Cloud Copy Gulf war illness (GWI) is a chronic condition that is considered multi-symptomatic, meaning there are a wide range of chronic and acute…
According to a recent article in NewsWise, researchers have discovered that families with the PCSK9 gene remain healthy through their eighties and nineties. The study has been published in the…
According to a story from GlobeNewswire, the biopharmaceutical company MediciNova, Inc. has announced encouraging results related in Optical Coherence Tomography (OCT) in a phase 2b clinical trial. This clinical trial…
by Lauren Taylor from In The Cloud Copy A cerebral venous thrombosis or CVT can happen when a clot is formed in the venous sinuses of the brain. This clot…
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