According to an article from Times-Call Regional News, a seven year old girl named Mila Makovec has just begun an experimental treatment for Batten disease. Originally from Boulder County, Colorado,…
A new study has revealed several complications of a multiple sclerosis treatment. The studies illuminate difficulties surrounding a powerful drug treatment and potential pregnancies. Keep reading to learn more about the…
According to a story from BBC, a former employer is paying for a woman's cancer treatment. 74 year old Pamela Stubberfield of Oxfordshire was diagnosed with mesothelioma. More than 80…
Pompe disease affects roughly one person in every 40,000. One form of the disease specifically develops within the first months of birth, or early on in childhood. Now, the first…
According to a story from the International Business Times, researchers have successfully grown kidney tissue that can filter and produce urine within a living organism. This has the potential to…
According to a story from Yahoo News, The family of Isla Caton, a three year old girl diagnosed with neuroblastoma, has raised enough money for her to travel to New…
At the beginning of February. BioPontis Alliance announced a partnership with Massachusetts General Hospital. Together, the two set their sights on Huntington’s disease. Specifically, they hope to develop new treatment options.…
The Mercury News originally reported that a new cannabis based drug found success with reducing epileptic episodes in patients with Lennox-Gastaut Syndrome. They hope to have the drug available on…
According to a story from MedicalXpress.com, a team of Chinese researchers successfully regenerated lung tissue in a patient using stem cells transplants. Although it is still in its infancy, growing…
According to a story from Business Wire, selumetinib, a drug in development for the treatment for neurofibromatosis type 1, was recently granted Orphan Drug Designation by the Food and Drug…
The Westmorland Gazette reports that a new drug called Perjeta, has been given the thumbs up to treat women with metastatic breast cancer in England. Metastatic breast cancer is when one's…
According to an article from Parkinson's News Today, a recent analysis testing transcranial magnetic stimulation demonstrated that the procedure was not effective in treating the depression that is a common…
According to a story from the Irish Mirror, eleven year old Cezy Fosca, who has a rare condition called Morquio syndrome, has lost access to the only drug available that…
A new digital platform has been created with hopes to assist cystic fibrosis (CF) patients at the comfort of their own homes, limiting hospital visits, reports Evening Standard. This new…
According to an article from globenewswire.com, the pharmaceutical company Amicus Therapeutics announced that the Food and Drug Administration (FDA) has the company's New Drug Application for migalastat with filing for…
One of the most impressive moments of childhood is when a young child takes his or her first steps. Natalie Essex, age four, loves to walk. For Natalie, spinal muscular…
According to an article from news-medical.net, a group of researchers from the Telomere and Telomerase Group at the Spanish National Cancer Research Centre have been able to pin down the…
According to a story from Specialty Pharmacy Times, medical professions are starting to recognize the need for a new standardized treatment plan for pediatric rheumatic diseases. Pediatric diseases are illnesses…
Little Natalie Essex was diagnosed with spinal muscular atrophy type 2 (SMA) when she was only a year and a half, reports CBC News. It all started when her mother, Meredith,…
According to a story from EurekAlert, a recent study published in the journal Pediatric Research reveals new protein biomarkers that researchers can use to evaluate how patients with progeria have reacted…
According to a story from biospace.com, a treatment developed by the pharmaceutical company Pfizer was given Breakthrough Therapy designation by the Food and Drug Administration (FDA). The drug is a…
According to an announcement from ema.europa.eu, the European Medicines Agency (EMA) recently granted market authorization for a new treatment for alpha-mannosidosis. The new drug is an enzyme replacement therapy called…
Maddie Holt from Everett Washington is a 5-year-old with severe disabilities. She can barely hear or see, and she certainly can't walk or talk, reports Maine Public. Unfortunately for her,…
According to a story from the National Hemophilia Foundation, the pharmaceutical company Novo Nordisk announced that its product REBINYN was now available for hemophilia B patients. The treatment is intended…
16-year-old Teenager Ciara Micks of Limerick, Ireland, tries to remain positive despite an unsettling situation regarding next steps to treat her EDS, Ehlers-Danlos Syndrome, reports Limerick Leader. Ciara deals with…
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