According to a story from the Canberra Times, Dan Gaffney, resident of the Blue Mountains in Australia, was denied access to a treatment that was helping to extend his life…
According to an article from kait8.com, the pharmaceutical company Yisheng Biopharma announced that YS-ON-001, a leading candidate for the company, received Orphan Drug Designation from the U.S. Food and Drug…
According to an article from brightsurf.com, a commonly used allergy medication called cetirizine (commonly marketed under the name Zyrtec) was able to prevent relapse in patients with neuromyelitis optica in…
Mesoblast Limited announced the primary endpoint success of a phase three trial on February 21st. The drug tested aims to help treat steroid refractory acute graft versus host disease. No…
Haley Hayes is a normal pre-teen, yet she suffers from Pompe disease. Pompe disease is a genetic condition, which causes muscle and organ impairment. Early diagnosis and enzyme replacement therapy…
According to an article from PRNewswire, recent research may have discovered why glioblastoma tumors develop resistance to treatment. Glioblastoma is a deadly form of brain cancer that is known for…
According to a story from bioportfolio.com, The California Institute for Regenerative Medicine has given $5.74 million to the City of Hope, a private, nonprofit clinical research center that is primarily…
A new cannabis treatment is going into trial in Australia to treat patients with Tourette syndrome, reports The Courier Mail. This will be the first study in Australia to use…
According to a story from wivb.com, a treatment for multiple sclerosis was recently recalled and taken off the shelves after some disturbing reports of side effects. The drug in question…
Biopharmaceutical company CorMEdix Inc. announced on Friday, February 23rd that its product taurolidine received orphan drug status from the United States Food and Drug Administration (US FDA). Taurolidine exists currently…
A new medical educational platform called the HealthVoyager has been released and is now being utilized following a collaboration with the Boston Children's Hospital and Klick Health, reports PR News…
You might think that completing cancer treatment and surviving the terrible experience would be the ultimate relief, yet, a new report shares the heightened stress cancer survivors face, reports CBC…
According to a story from macleans.ca, eight-year-old Mason Stewart has been dealing with the effects of spinal muscular atrophy since he began to walk; he developed an unusual walking gait…
England’s National Institute for Health and Care Excellence (NICE) recently approved three new thyroid cancer treatments for their National Health Service (NHS). The new treatments provide a wider variety of…
According to an article from kait8.com, the pharmaceutical company Polaryx announced that its experimental drug PLX-200 has received Orphan Drug Designation from the European Medicines Agency (EMA) for the treatment…
Fashion blogger Yavanna Keogh who runs Makeupmonster just took to social media the devastating news of her son's recent diagnosis, first reported by Mirror. Yavanna and her partner from Dublin,…
According to a story from MSN, Heather Huus is living life without a stomach. This may seem impossible, but keeping her stomach could have made things far worse for her.…
Corbus Pharmaceuticals has received the Development Award presented by the Cystic Fibrosis Foundation, along with $25 million to support an upcoming study, reports Financial Buzz. Corbus plans to test out…
According to Yahoo! News UK, cancer survival rates have increased over the passed ten years. However, the progress hasn't been evenly distributed across the board of varying cancers. According to…
An exciting "win" in the relatively common glaucoma department could also mean a "win" for rare childhood glaucoma patients. According to an article from MedicalXpress, two recently approved treatments for…
When Jonathon Hume went to a general practitioner in college with his symptoms: feeling lethargic and extremely sleepy throughout the day, missing classes, and even sleeping through exams, he was…
Researchers at UC-Davis Veterinary Medical Teaching Hospital look to utilize dogs and cats to help find rare disease treatments, reported The Daily Beast. Recently, two bulldogs, Darla and Spanky, with…
Getting back to the workplace post-cancer treatment is known to be good for cancer survivors, as they establish a normal routine again, but with that said, there are many factors…
The Imperial College of London recently began development of a body suit to improve treatment of Duchenne muscular dystrophy. The suit uses a unique artificial intelligence interface to collect and…
Madrigal Pharmaceuticals recently brought a new familial hypercholesterolemia drug to clinical endpoint. The drug is currently being tested as MGL-3196. Here's what you need to know about the new drug.…
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