According to a story from cnbc.com, the pharmaceutical company Novartis recently announced that their anticancer drug Tasigna has been approved for the treatment of patients one year or older that…
According to a story from Financial Content, the drug company Arena Pharmaceuticals recently announced that its data results from Phase II clinical trials has been positive. The trial in question…
According to a story from CBS DFW, doctors have begun to test the use of fluorescent dyes in order to detect hidden cancer tumors. So far, the dyes appear to…
According to a story from financialbuzz.com, the biotechnology company BIOPHYTIS has submitted documentation for orphan drug designation from the European Medicines Agency (EMA). This designation will be for Sarconeos, a…
According to a story from globenewswire.com, the pharmaceutical company Amicus Therapeutics recently announced that its drug Galafold had received official approval for public use in Japan. Galafold is the first…
Erin Gard and her mother, Joanne Guthrie-Gard, already spent many years of their lives searching for an effective epilepsy medication for Erin. However, once they found it, they lost access…
According to a story from Medical Xpress, two new treatments were able to slow down the worsening of symptoms associated with muscular dystrophy in a mouse model study. Tamoxifen and…
Vanderbilt University Medical Center researchers have discovered a new method of searching existing electronic medical records to help identify genetic diseases in larger populations, reported EurekAlert!. Many people who may…
When Mac Grieb was just a one-year-old he already had two open heart surgeries and doctors said that he would need another in his teenage years, reports The Inquirer. Last…
According to a story from Walcha News, Felicity Nivison first began feeling paralysis and pain in her feet and hands. Soon, the symptoms spread to her legs and she was…
According to a story from People, parents Lester and Noreen Jessop from Utah recently discovered that all three of their children have a rare, life-threatening disease called pantothenate kinase-associated neurodegeneration. Their firstborn…
According to a story from pharmiweb.com, the pharmaceutical company Ovid Therapeutics announced recently that the U.S. Food and Drug Administration (FDA) has given its drug candidate OV101 Fast Track designation…
According to a story from sciencedaily.com, new and improved standards of treatment are allowing patients with Duchenne muscular dystrophy to have longer lifespans than in the past. By all accounts,…
26-year-old Rebecca Smith's pregnancy was going as smooth as can be until she was 8-months pregnant, reported Hertfordshire Mercury. Rebecca discovered a lump on her neck and went in for…
Just recently, MMJ International Holdings announced that MMJ Bioscience has received proper Canadian licensing to grow cannabis specifically to develop cannabinoid medicines to treat patients battling multiple sclerosis and Huntington's…
According to a story from guttmacher.org, the U.S. Department of Health and Human Services proposed a host of new regulations purported to enforce over 20 federal provisions related to "conscience…
According to a story from PR Newswire, the pharmaceutical companies Sanofi and and Regeneron Pharmaceuticals are implementing a plan to make Praluent injections more accessible and affordable for patients with…
According to a story from news-medical.net, researchers from The Scripps Research Institute have successfully outlined a new path for the treatment of Charcot-Marie-Tooth disease subtype 2D (CMT2D). The scientists hope…
The apparent goal behind the current Right to Try legislation is to create better access to life saving medication. Many people are excited about the possibilities such a bill could…
According to a story from pharmpro.com, the pharmaceutical company Abeona Therapeutics announced that it has been given Rare Pediatric Disease Designation for its ABO-202 program by the U.S. Food and…
According to a story from Financial Buzz, the pharmaceutical company Proteostasis Therapeutics recently announced that the company's experimental treatment PTI-428 was granted Orphan Drug Designation by the FDA. PTI-428 is…
According to a story from pm360online.com, some recent studies from Scandinavia are serving to highlight the lack of advances in treatment for psoriatic arthritis. While other types of arthritis have…
Losing a child has to be one of the most heart-wrenching experiences a family can encounter, yet losing a child when it could have been prevented is even more devastating.…
According to a story from the Clarion Ledger, surgeons at the University of Mississippi Medical Center are now trained to conduct a minimally invasive procedure to relieve the symptoms of…
According to a story from pharmavoice.com, the pharmaceutical company Cadent Therapeutics has announced the beginning of the Phase I clinical study for its drug candidate CAD-1883. The therapy is a…
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