According to a story from EurekAlert!, scientists from UCLA have developed a new method of delivery for gene therapies called nanospears. These structures could allow for more accurate and precise…
Thanks to a local physician’s group in Baton Rouge, patients with amyotrophic lateral sclerosis (ALS) no longer face lengthy drives to receive treatment. The clinic serving the Baton Rouge area…
According to a story from BioSpace, the U.S. Food and Drug Administration has given Fast Track designation for nintedanib, which is undergoing testing for the treatment of systemic sclerosis with…
Primary immunodeficiency diseases account for hundreds of rare and chronic diseases. In children, this may mean that their immune system is non-existent or doesn't perform as expected. To learn more…
According to a story from raredr.com, The U.S. Food and Drug Administration (FDA) has recently approved Hizentra as a maintenance therapy for patients with chronic inflammatory demyelinating polyneuropathy. Hizentra is…
According to a story from raredr.com, the FDA had to order the cessation of Phase II/III trials for the microdystrophin transfer therapy SGT-001, which was in development for the treatment…
A team lead by geneticist Christopher Gregg from the University of Utah conducted a study on elephant genes that discovered why elephants don't get cancer, reported by News 4 Tucson.…
Recent research by a team at University of Cambridge suggests that a patient’s skin cells could be the key to treating multiple sclerosis. Reprogramming one’s own skin cells, the research…
According to BelfastLive, Darren and Danielle Gibson, the parents of little six-year-old Sophia battling Dravet syndrome, traveled out of the country in search of the care she needs. For the…
According to a story from The Globe and Mail, doctors were baffled after four young women who had a deadly and rare type of ovarian cancer were saved with an…
New technology always peeks out from around the corner. Modern medicine chugs along just fine, but some people think precision medicine could be the future. Precision medicine is an individualized,…
According to a story from drugs.com, kids and teenagers with chronic kidney disease (CKD) may develop problems with learning and cognition, a new study suggests. Researchers emphasize that patients on…
According to an article from Medical Xpress, a recent study suggests that an anti-cancer drug commonly used to treat leukemia may be effective in treating a rare form of ovarian…
Novartis and Pear Therapeutics have joined forces to develop digital therapeutic software applications to treat patients with schizophrenia and multiple sclerosis, reports World Pharma News. Novartis is known for the…
Clearside Biomedical recently developed a new treatment for impaired vision. The drug, tested in a group with uveitis, succeeded not only in treating symptoms of disease, but also resulted in…
According to a story from Medical Xpress, the addition of crizotinib with radiation therapy could help reduce hearing loss associated with the treatment in patients with neurofibromatosis II. Crizotinib is…
According to a story from the Vancouver Sun, 11-year-old Jaylene Prime from British Columbia was able to obtain access to a critical treatment for her juvenile idiopathic arthritis. The drug,…
The Southern Daily Echo originally reported that a majority of pancreatic cancer patients don't receive life-extending treatment after diagnosis. Recently, the Pancreatic Cancer UK charity reported that only a small…
Scientists in California at Salk Institute for Biological Studies are currently developing a drug that can mimic the effects in the body usually obtained from exercise, reports the National Post.…
Dr. Woodrin Wright studies telomeres – the part of our DNA that determines aging. It's also involved in some cancers. It seems like a cruel irony then that Dr. Wright…
According to a story from fiercebiotech.com, the gene therapy startup Generation Bio managed to fundraise $100 million in a little over a month. In its prior series A round of…
According to a story from Financial Buzz, the pharmaceutical company Evoke Pharma announced that the U.S. Food and Drug Administration has approved a small business waiver for Gimoti, a nasally…
According to a story from kait8.com, the FDA recently approved donor screening tests for blood donors that will test potential donors for the parasite Babesia microti, a type of protist that can…
According to a story from Morningstar, the pharmaceutical company Emerald Health Pharmaceuticals announced that its drug candidate EHP-102 was given Orphan Drug Designation by the U.S Food and Drug Administration…
The day after Christmas in 2016 brought a post-Holiday surprise to many in the U.S. with spinal muscular atrophy. December 26, 2016 marked the day that Spinraza was approved by…
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