Cannabidiol Oral Solution Granted Fast Track Application for Prader-Willi Syndrome
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Cannabidiol Oral Solution Granted Fast Track Application for Prader-Willi Syndrome

Prader-Willi syndrome is a rare condition which causes the body to feel insatiable hunger, regardless of how much a patient eats. Treatment options are currently inadequate for many patients. Today,…

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Recent Study Results Reveal New Possibilities in Treating Paroxysmal Nocturnal Hemoglobinuria (PNH)
PNH causes the immune system to destroy red blood cells. Source: pixabay.com

Recent Study Results Reveal New Possibilities in Treating Paroxysmal Nocturnal Hemoglobinuria (PNH)

On December 11, Alexion Pharmaceuticals, Inc. released dose-ranging data from a recent clinical study involving treatment with ALXN1210, which is an investigational long-acting C5 complement inhibitor meant to treat sufferers…

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Study Of Thrombotic Thrombocytopenic Purpura Medicine Demonstrates Safety
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Study Of Thrombotic Thrombocytopenic Purpura Medicine Demonstrates Safety

Caplacizumab is a medicine that has been developed to treat acquired thrombotic thrombocytopenic purpura (TTP). TTP causes serious symptoms. such as thrombocytopenia, a condition in which a patient doesn't have enough platelets. A…

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Study of LJPC-401 Treatment for Hereditary Hemochromatosis Launches into Phase II
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Study of LJPC-401 Treatment for Hereditary Hemochromatosis Launches into Phase II

Hereditary hemochromatosis is a genetic form of a condition in which the body builds up too much iron. To read more about hemochromatosis, click here. La Jolla Pharmaceutical Company has…

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ICYMI: FDA Makes History Aproving a Gene Therapy That Can Improve Childhood Blindness
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ICYMI: FDA Makes History Aproving a Gene Therapy That Can Improve Childhood Blindness

According to The Washington Post, on Tuesday the Food and Drug Administration, FDA, made history by approving a gene therapy for childhood blindness, which will change the lives of many…

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