Researchers from St. Jude Children's Hospital might have just developed a new gene therapy that can build a healthy, functioning immune system for patients suffering from severe combined immunodeficiency, SCID,…
London specialists at the King's College hospital believe they should take an 11-month-old baby Isaiah suffering from multiple diseases off life support to avoid any further pain, reported The Guardian.…
Last month, the pharmaceutical company Sarepta Therapeutics announced the long awaited results of a study that measured lung function in patients with Duchenne muscular dystrophy (DMD) after they took eteplirsen,…
The Australian government has announced that almost that new treatments worth $300 million are being added to the Pharmaceutical Benefits Scheme. This program provides subsidized medical treatments to citizens of…
According to an article from the Chicago Tribune, many medical specialists are coming to the realization that the eligibility criteria for clinical trials should be reassessed. The problem is that…
Minoryx Therapeutics is on their way to making strides for patients with adrenomyeloneuropathy, also known as AMN, reports Labiotech. They just started their phase II initiative to test patients for…
A recent study conducted by researchers from National University of Singapore Medicine laboratory shows that eating vegetables, specifically broccoli, might prevent and even kill cancer cells that develop into colorectal…
A little more hope is given to individuals suffering from Lennox-Gastaut syndrome and Dravet syndrome as GW Pharmaceuticals shared the U.S. FDA will indeed be accepting their application for potential…
Happy Friday Patient Worthians! Believe it or not, we've almost made it through the first month of 2018! This week, we have a story of a young girl with Sanfillipo…
For many - leprosy is nothing but an antiquated disease from biblical times with no present-day relevance. But in fact, nearly 150 to 250 people in the United States and 250,000 around the…
Many cancer and blood specialists will not have encountered systemic mastocytosis. A new drug targets the underlying defect of the disease and will help put doctors on the lookout. Keep…
It's a good time to check in on your eye health because January is Glaucoma Awareness Month! More than 3 million people in the United States have glaucoma - and…
Most disabilities in Pakistan are caused by three diseases: Spinal Muscular Atrophy, Spinal Cord Injury, and stroke. With this in mind, a group in the country’s capital has launched the…
According to a story from the Murray Valley Standard, Lucia's parents Julie and Peter knew within weeks after her birth that something was wrong with their newborn baby's head. Although…
January is Thyroid Awareness Month! It may be difficult to find time to learn a little more about your body and health tips - but since it's Thyroid Awareness Month,…
Living with the rare condition subglottic stenosis is never easy, especially when you're trying to keep up with your little boy. Caledon Enterprise reported that Emily Rogers does just that. She…
David Fogel's aunt was diagnosed with an advanced stage of stomach cancer when she was just fifty-six years old. Constantly dealing with severe pain and the side effects of treatment,…
Out-of-pocket expenses for rare disease are astronomical, and the Ministry of Health (MOH), is taking time to find a more positive way to help benefit children and their families burdened…
According to an article from Vanguard, only a year after Pat and Ken were married, Ken was diagnosed with multiple sclerosis. He was 29 years old. They had planned to…
A phase three clinical study is beginning for a new glioblastoma treatment. The new drug is called VAL-083 and is specially designed for treatment of late-stage glioblastoma. The study will…
Everyone is guilty of blaming back pain on stress stemming from work and life in general, but there becomes a point when one has to realize something might just not…
According to a story from wqad.com, transplants are responsible for saving thousands of lives. Often, transplants are the last resort in diseases that have become to severe to treat effectively.…
On the pages of the Abby Grace Foundation website, you will find over twenty beautiful pictures of different children. Most of the children are smiling. One looks into the camera…
25-year-old Zoey Wright is a real force of nature! Having been diagnosed with the rare disease ulcerative colitis she found herself dependent upon a colostomy bag, yet that didn't stop…
According to a story from Oklahoma's Nursing Times, Lori Garman, a scientist at the Oklahoma Medical Research Foundation, was selected for The Foundation for Sarcoidosis Research Fellowship Program Award. The…
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