According to an article from seattletimes.com, a homeless man's fight with cancer may actually improve his dire circumstances. Alan Brooks, a homeless man who was down on his luck, had…
The FDA approved a human study to be conducted by Swedish Orphan Biovitrum AB to treating mucopolysaccharidosis type lllA patients with a new drug called SOB1003, reported European Pharmaceutical Review. Not only…
Scientists in the UK are hopeful that they have discovered a new tool in the battle against brain cancer. The surprising solution is a virus. Ten patients in the UK…
According to a story from IBD News Today, the Food and Drug Administration (FDA) has just issued approval for the pharmaceutical company Immunic Therapeutics to move forward with Phase II…
The holidays are a little extra special for best friends Diana Caldon and Stephanie Smith. As optimistic cancer survivors, these two refuse to let holidays get away from them and…
January is National Birth Defects Prevention Month! A birth defect is defined as a problem that happens while a baby is developing in the mother's body. Most birth defects happen during the…
The Alabama Rare Disease community has come together to host a special week in honor of the upcoming date February 28th, 2018, which is now the official International Rare Disease…
When Terry Jo Bichell learned her son was diagnosed with Angelman syndrome, but little knowledge existed on the disease, she decided to get her PhD and do research herself, reported…
According to a story from PR Newswire, the pharmaceutical company Biohaven announced that they have received clearance from the Food and Drug Administration (FDA) to begin work on its clinical trials…
Ded Rranxburgaj, 48, currently living in Southgate, Michigan is being threatened with deportation, although his wife suffering from multiple sclerosis, reported MSN News. While fighting the deportation from every angle, Ded…
Patients suffering from the rare blood disease, hemophilia, deal with daily demands of their treatment. A recent study supports self-infusion for these patients, reported Harrison Daily Times. Self-infusion is when…
According to a story from ibtimes.co.uk, Sue Cox, a 65 year old Welsh woman from Cwmbran, has sought alternative methods for dealing with the worst symptoms of her multiple sclerosis.…
Reported by Strait Times, it was announced by Ministry of Health last week that there may be a potential fund developed to help children who suffer not only from a…
Tomorrow is Moebius Syndrome Awareness Day! Moebius Syndrome Awareness is celebrated globally each year - with the goal of raising awareness about this rare condition and to educate the many…
On January 17th, Parent Project Muscular Dystrophy announced that the first patient had been treated with a new gene therapy. The therapy developed specifically for Duchenne muscular dystrophy is known as…
According to an article from rdmag.com, a new form of treatment could allow for organ tissue to regrow to a normal level in patients with conditions in which organs are…
The gene therapy development company, AveXis, Incorporation, just announced that they will be expanding their clinical trial development program for the potential gene therapy treatment: AVXS-101, reported Globe News Wire.…
According to BBC News, a new universal blood test is receiving a lot of buzz due to it's potential to detect early stages of cancer. A research team at John…
The Driscoll family is left devastated and shocked after receiving a letter from social services that states the government could be taking their daughter, who is suffering from Rett syndrome,…
Potentially good news arrived for patients with hereditary TTR amyloidosis, as the treatment drug inotersen received it's New Drug Application approval and will go into review by the U.S. Food…
According to an article from PRNewswire, the drug MVASI (biosimilar bevacizumab) was just granted marketing authorization by the European Commission. Developed by Amgen and Allergan, this treatment has been approved…
According to an article from bioportfolio.com, the pharmaceutical company Ophthotech announced that the first of its patients are being enrolled in its Phase 2b clinical trial. This trial is meant…
According to a story from Drug Discovery & Development, The European Commission announced its approval of marketing certification for OCREVUS, a treatment for relapsing types of Multiple Sclerosis (MS). The…
19-year-old Jonathan Inkin created a "20-strong" bucket list with intention to cross them all off before his birthday. Thanks to the help of celebrity Toff (Georgia Toffolo), the winner of…
Tiffany and Caleb isn't your typical engaged couple. They are passionately in love and excited for their wedding, but their romance could literally end any moment. NBC 5 Chicago reported…
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