Reported by Fox 2, Anthony Anzell doesn’t let his rare genetic disease hold him back. Anthony is an extreme athlete who just swam 19 miles, the entire length of Torch…
Even though most in the medical field suggest that people think about their wishes as to how to handle end-of-life decisions, and complete the paperwork to be sure their wishes…
The Hempel family decided to take action against Vtesse and Sucampo Phamaceuticals who allegedly stole and sold their private information for profit, reported Forbes. The Hempel family has two twin…
Even after the third denial from the U.S. FDA, Food and Drug Administration, PTC Therapeutics Incorporation will not stop fighting for the drug Translarna that they believe will help patients…
A team of scientists recently developed an electronic nose that detects Crohn’s disease and ulcerative colitis. Continue reading below, or follow the original story to learn more about this intriguing…
The Wahlstrom family of four, is getting a miraculous gift to help care for their two children suffering from Batten disease, reported CBS Minnesota. With the love of their local…
The FDA, US Food and Drug Administration, unanimously agreed upon the recommendation for a new gene therapy that treats a rare form of blindness, reported ScienceNordic. Spark Therapeutics, a biotech…
There is potential for a new treatment for Duchenne muscular dystrophy. Duchenne muscular dystrophy (DMD) is a genetic disorder characterized by progressive muscle degeneration and weakness.To learn more about this…
TGIF, Patient Worthians! This week, kids went to bed wearing inside out pajamas and wishing for snow. Their wishes came true-- and so did the wishes of many rare disease…
According to an article from One News Page, the biopharmaceutical company Motif Bio was generously presented with an award from the Cystic Fibrosis Foundation. The award came in the form…
If you live near Pompano Beach in Florida, the Water Balloon Bulls-eye charity event is not to be missed, reported Sun Sentinel. The event is focused on raising money, as…
I know you’re fighting hard//I see your battle scars It’s clear you’ve come so far//You’ll grow stronger Alone, these words may feel like just expressions of encouragement; a…
Coffee or tea is the preferred way for many people to start their morning. That extra boost of caffeine just seems to get things rolling. New research suggests that caffeine…
I have fantasized at times about living in a different era. How exciting to live in the times of knights in shining armor and ladies in fancy dresses in a…
CISCRP, The Center For Information & Study On Clinical Research Participation, is a unique and one-of-a-kind non-profit focused on clinical trial education. CISCRP is wants to bring the need for…
A recent study suggests therapy dogs may lower stress among cancer patients and their families. The study notes especially how useful this could be with young patients. Bryce and Mitchell,…
GW Pharmaceuticals reports that Epidiolex, a cannabidiol based drug, had its NDA (New Drug Application) accepted for priority review by the Food and Drug Administration (FDA). The drug is intended…
Blessings amongst the hardest time in Jessica Boesmiller's life came in the form on twins, reported News.am. 37-year-old Jessica is a mother of four and recently learned in November that…
Days in 2018, we have some great statistics on 2017! According to the United Network for Organ Sharing (UNOS), over 10,000 organ donations were made, marking the first year that number has been…
Deciphera Pharmaceuticals recently announced the initiation of a Phase 3 clinical study. The study aims to investigate the safety and effectiveness of a new drug targeting gastrointestinal stromal tumors. Keep…
The Loma Linda University Eye Institute in California performed its first-ever procedure using a FDA-approved procedure, which can deter the effects of keratoconus - a rare progressive disease of the cornea,…
According to a story from financialbuzz.com, the pharmaceutical company MabVax Therapeutics just announced initial dosing for patients and the completion of enrollment for its Phase I trial study. The study…
The Mastocytosis Society is an amazing organization that brings focus to patients with mastocytosis and mast cell activation diseases. They hope to bring awareness, as well as education to patients,…
Natasha Coates has a lot more to be cautious of than most people. Anything she eats or drinks could be lethal. She’s even allergic to her own hair and tears…
America first started noticing South African runner Annie Bothma at the Roy Griak invitational in 2015. She came in third! Not only is she talented, but her preferred running technique…
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