According to BioPortfolio, the company UniQure has recently announced that the first hemophilia B patient has been enrolled in their Phase III study of the treatment AMT-061, which is an…
According to a story from CNN, Nick Foles, who plays for the Philadelphia Eagles, helped lead the team to victory at the Super Bowl, and was awarded MVP for the…
If you look on Ed Sheeran's Instagram you will see a recent photo of him and a beautiful eleven-year-old fan. But this is not just any fan-- the picture holds…
A recently published study found that, out of the people studied, young cancer survivors were more likely to develop endocrine diseases than people who had no history of cancer. The…
Researchers investigating the symptoms of testicular cancer have published their results in the British Journal of General Practise. Their study showed that testicular enlargement from a lump or swelling is…
Duncan Avery is father to two children, Kalea, and Noah. At age six, doctors discovered Kalea had a tumor in her brain. They would successfully remove it via surgical methods.…
According to a story from Jewish Community Voice, the BRCA Founder Outreach Study, which is a national, cancer-focused research study, is offering free screenings for people of Ashkenazi Jewish descent.…
Miracle Flights help children to fly to access medical treatment. They work to support people like Shelby, who was diagnosed with alveolar soft part sarcoma at the age of seventeen.…
Most of us are familiar with Parkinson's Disease. Parkinson’s disease is a central nervous system disorder affecting movement. It is a progressive disease and develops gradually, sometimes starting with a subtle tremor in…
According to Medical Xpress, Chris Jones from the Institute of Cancer Research in the UK has delved into the complexities of the rare childhood brain tumors called diffuse intrinsic pontine…
According to a story from sciencedaily.com, recent research has revealed the mechanism that causes hypokalemic periodic paralysis, a rare condition that causes patients to experience sudden, severe muscle weakness. The…
Who needs a shot of feel good today?! Young Skye Savren-McCormick was diagnosed with juvenile myelomonocytic leukemia in 2016 and required a bone marrow transplant - and Hayden Hatfield Ryals…
According to a story from govloop.com, Dr. Daniel Kastner, the Scientific Director for the Division of Intramural Research at the National Institutes of Health (NIH), has committed his career to…
Helena Baker is the Vice President of Clinical Strategy at Medical Research Network, a Nurse, and also, a rare disease patient. I had the opportunity to interview her for a…
According to a story from medicalxpress.com, early tests of a gene therapy for X-linked myotubular myopathy are showing promising results. This could represent a major breakthrough for this disease, which…
A researcher from the University of Alabama at Birmingham is working on how to improve treatment for patients with status epilepticus. The original article can be read here, at UAB…
The final results from a study of the experimental drug tegsediTM (inotersen) for the treatment of patients with hereditary ATTR amyloidosis with polyneuropathy have been published. The original article can be…
Cleveland Clinic’s first every three-way kidney transplant has taken place. It involved six people in total: three donors and three recipients. The full article can be read here, at the…
When you think of arthritis, naturally the first thing that comes to mind is an older person - and with good reason, since artists is more common in people over…
According to PRNewswire, Beverly Hills, and Frankfurt based INFUSIO donated $5000 each of their patient’s Lyme disease treatment in May. Interest in the program was high. As a result, INFUSIO…
For any John Oliver fans out there, you know his thing is deep-diving into topics of importance - from beauty pageants to international elections to failing American infrastructure - just…
The experimental drug olinciguat (IW-1701) has been granted Orphan Drug Designation by the U.S. Food and Drug Administration (FDA) for the treatment of sickle cell disease. The full article can…
The Children’s Hospital Colorado has announced that it will part in a Phase 3 clinical trial for an experimental new cystic fibrosis therapy. The full article can be found at…
Happy Independence Day Weekend! As the firework shows wind down, we want to wrap up the week with three great contributor stories, and one research update. First, we have some…
Dewayne Johnson used to work as a school groundskeeper. Now, some days, he can’t manage to speak as a result of the cancer he lives with. Now, despite professional expectations…
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