In 2016 the Centers for Disease Control verified that Zika virus caused birth defects such as microcephaly. This shocked the world. We witnessed the first mosquito-borne disease known to result…
Scientists in California at Salk Institute for Biological Studies are currently developing a drug that can mimic the effects in the body usually obtained from exercise, reports the National Post.…
Rare disease patients remain one of the most underserved medical populations, and they often have to deal with debilitating symptoms or complications that can make daily life difficult. For example,…
Lyndsey Rowe wanted to make sure her son left a legacy. Lloyd always wanted to help people, but a lost battle against brain cancer prevented him from doing all of…
According to a story from macleans.ca, after beginning to develop problems with mobility such as climbing stairs, Julie Mason of Montreal endured years of confusing tests before doctors were able…
According to a story from the Wall Street Journal, the U.S. healthcare system might be able to learn a thing or two from Netflix. A well understood aspect of healthcare…
CRISPR gene editing technology is still mostly in its infancy, but the new tool is already causing a lot of excitement, particularly in the treatment of genetically-linked diseases. A recent…
According to a story from PressReleasePoint, a new partnership has developed to generate artificial intelligence technology that will help diagnose people with a variety of rare diseases. The partnership consists…
Dr. Woodrin Wright studies telomeres – the part of our DNA that determines aging. It's also involved in some cancers. It seems like a cruel irony then that Dr. Wright…
According to a story from fiercebiotech.com, the gene therapy startup Generation Bio managed to fundraise $100 million in a little over a month. In its prior series A round of…
According to a story from Financial Buzz, the pharmaceutical company Evoke Pharma announced that the U.S. Food and Drug Administration has approved a small business waiver for Gimoti, a nasally…
Ellie White is everything you would want in an 18-month-old daughter, fun, playful, and full of life-- yet not too long ago her family discovered she had a rare disease,…
Just yesterday, the incredibly successful actor Irrfan Khan, announced on twitter that he just found out he has a rare disease, reported The Guardian. Khan has appeared in over 100…
According to a story from kait8.com, the FDA recently approved donor screening tests for blood donors that will test potential donors for the parasite Babesia microti, a type of protist that can…
Macey Brietenback continues to defy all odds. Originally reported by CBS Baltimore, the teenager lives with a condition that prevents her from digesting food. Even though it has given her…
Happy Friday, Patient Worthians! Today, we're highlighting a story about the donors who sacrifice their kidneys for rare patients, an update on CF research, and an exciting orphan drug designation.…
According to a story from Morningstar, the pharmaceutical company Emerald Health Pharmaceuticals announced that its drug candidate EHP-102 was given Orphan Drug Designation by the U.S Food and Drug Administration…
The day after Christmas in 2016 brought a post-Holiday surprise to many in the U.S. with spinal muscular atrophy. December 26, 2016 marked the day that Spinraza was approved by…
According to a story from the Canberra Times, Dan Gaffney, resident of the Blue Mountains in Australia, was denied access to a treatment that was helping to extend his life…
This year has brought an especially nasty and dangerous strain of the flu. Nobody wants the flu, but contracting the virus while suffering from an underlying condition can be more…
According to a story from Science Daily, researchers at the University of Michigan have discovered why it is possible for basal cell carcinomas, a common form of skin cancer, to…
According to a story from the Baylor College of Medicine Blog Network, Terry Lim, a women with familial hypercholesterolemia, views her condition with a new perspective after participating in a…
According to a story from the Daily Post, Katie Roy and Tjay Narciso were horrified when doctors told them that their new born daughter Kaila will only survive for a…
New medicines for Parkinson’s may be around the corner. The United States Food and Drug Administration (US FDA) recently approved one drug, and accepted application another. Both new drugs treat…
For so many of us, a good night's sleep is a refuge; from our long hectic days, from our piling problems, or even from the stresses of managing our rare…
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