Patient Worthy is proud to announce we are participating in Patients as Partners EU in London, UK on January 23rd. Patients as Partners EU represents the only conference opportunity in Europe…
Nursing student Jess Boxley could be blind if she didn't see a doctor for her extreme headaches and neck pain, reported The Huffington Post UK. Jess, at a young 22-years-old,…
Margarita Matias could not believe her eyes when she walked into the newly renovated bathroom. Her old bathroom was far from ideal, and often leaked. The new arrangement is optimized…
According to a recent article from indiatoday, a new study has revealed information about how osteosarcoma and other cancer cells manage to survive in the body. The new research suggests…
According to an article from businesswire.com, the pharmaceutical company Odonate Therapeutics announced the beginning of CONTESSA, a phase three study of the treatment tesetaxel and its function in patients with…
Patients suffering from sickle cell disease, SCD, might just be getting news they've been waiting to hear for a long time. Just this week, the U.S. Food and Drug Administration…
At three months old, Emily's mouth hurt. Her first tooth started coming in. Her parents immediately knew that something was wrong. Three months later, the family received dire news about…
While it's general knowledge that working out is a huge plus for a healthy life, many questioned whether it was positive or dangerous to individuals with rare diseases. Yet, BMC…
According to a story from philly.com, many people with severe forms of brain cancer are not receiving sufficient hospice treatment, according to a recent assessment. The study took data from…
According to a story from financialbuzz.com, the pharmaceutical company AveXis, Inc., is planning to begin preparations to submit a Biologics License Application (BLA) to the Food and Drug Administration for…
According to a story from the Chicago Tribune, Ben Barres, a widely renowned neurobiologist and researcher, passed away at age sixty-three after fighting pancreatic cancer. Mr. Barres was credited with…
5-month-old baby, Rohaan's, life was spared when he recently underwent surgery to treat his rare congenital heart condition, surgery that almost didn't happen, reported Times Of India. His parents, Muhammad…
Watch Prof. Charles Craddock discuss important and heartening results he and his team presented at the American Society of Hematology 2017 Annual Meeting and Exposition in Atlanta, GA - regarding whether there…
When you are in the midst of difficult times in your life, what do you do to make it through? Do you try and find a way to hide out…
According to a story from prnewswire.com, the experimental treatment SPR001 was just granted orphan drug status by the Food and Drug Administration (FDA). The new treatment is currently being developed…
Patient Worthy recieved a note from CMT Warrior and Patient Worthy Contributor Quentin Martin of a worthwhile cause, that we think all our readers should know about! Quentin writes: If…
Nikki Oosthuizen gave her 16-year-old daughter, Kim, a kidney as she suffers from a rare kidney disease, yet only four days later the disease returned and destroyed her kidney function…
2017 was a challenging year for 10-year-old Zach Pickard, but at first glance of his smile and rolling laughter, you would never expect it. Zach is among 144 children in…
Cycle Pharmaceuticals shook hands with US-based firm, Aprecia Pharmaceuticals as they agreed to develop and commercialize treatments for rare diseases using the advanced technology of 3D printing, recently reported Cambridge…
Gene therapy has successfully made its presence known in the medical field this last year, reported ABC News. Dr. Francis Collins of the National Institutes of Health isn't afraid to…
A recent study has revealed a possible mechanism for the repair of nerves damaged by multiple sclerosis. Research at the University of California has found that gene expression in certain…
Organovo Holdings recently stated that its 3D bioprinted therapeutic liver tissue was granted orphan drug status by the Food and Drug Administration (FDA). Taylor Crouch, the company CEO, was excited…
A young boy suffering from a rare disease was faced with a bundle of surprises, including a surprise trip to Disney World, just in time for the holidays. The Burlington…
The world of rare disease is seeing a ray of sunshine with a viable partnership. Two powerhouses of patient advocacy are uniting together to bring about change, awareness and cure-searching.…
Poor mental focus may be a contributing to the paralysis that commonly occurs after a stroke, according to a new study. A person who has had a stroke, when the…
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