As you know, COVID-19 has fundamentally changed our daily life. What began as a novel coronavirus in Wuhan, China has developed into a global pandemic: 9 million diagnosed cases…
According to a press release from HemoShear Therapeutics, the company has recently received official clearance from the US Food and Drug Administration (FDA) in regards to its Investigational New Drug…
Patients with Parkinson's disease or essential tremor are no strangers to shaking or tremors. In fact, for patients with Parkinson's disease, their tremor progresses throughout the course of the…
In a Business Wire press release, the Canadian NASH Network (CanNASH) shared the results of a recent study predicting a severe increase in cases of nonalcoholic fatty liver disease…
"I thought it was a hernia." When George Benson experienced lower abdominal pain in 2009, at age 51, he wasn't concerned. He was a truck driver, artist, and family…
According to a story from Parkinson's News Today, a recent study has found that a combination treatment of levodopa and carbidopa delivered to the intestines could be an effective treatment…
COVID-19 has now taken hold in over one hundred eighty countries. According to a recent article in The Lancet, in May of 2020, the United States reported the highest…
Osteoporosis is known to affect over two hundred million people worldwide. According to a recent article in the Endocrinology Advisor, fractures of the spine or hip due to reduced…
It's no surprise that our family can have an impact on how we grow up: our behaviors, beliefs, attitudes, values. But perhaps most importantly, our family history impacts our…
If you've been overwhelmed by the news and are looking for a feel-good story, you've come to the right place! Five years ago, when they were just 5 years…
As reported in Business Fortnight, the top level gene therapy company AVROBIO has announced successful clinical trials for investigational drugs for Fabry disease and cystinosis. The CEO of AVROBIO, Geoff…
The Rare Diseases Clinical Research Network (RDCRN) has recently launched a survey aiming to assess the impact of COVID-19 on the rare disease patient community. This initiative is important as…
A recent Italian study sought to understand how patients with asthma and chronic rhinosinusitis with nasal polyps (CRSwNP) compared to patients with asthma without any other condition. They examined…
Cures Within Reach is an organization that aims to help patients by repurposing research. They work towards getting treatments quickly and safely in an effort to aid those who need…
According to a story from BioSpace, the biopharmaceutical company Dicerna Therapeutics, Inc. has announced recently that the US Food and Drug Administration (FDA) has granted Rare Pediatric Disease designation to…
Earlier this year, The Leukemia & Lymphoma Society hosted a presentation by Dr. Eunice Wang, Clinical Leukemia Service, Professor of Oncology, Roswell Park Comprehensive Cancer Center. Dr. Wang’s presentation…
If you're like me, your life has changed immensely over the past few months. COVID-19, a novel coronavirus with 8.39 million diagnoses worldwide, has kept us inside and changed…
According to the Cambridge Network, Cambridge University Hospitals NHS Foundation Trust (CUH) is starting a new clinical trial to test two experimental treatments for COVID-19. The trial, called TACTIC-E,…
Last week, I had the privilege of attending a webinar organized by Research!America titled Partnership, Progress, Pandemic: The Impact of COVID-19 on Medical Discovery. As implied in the title, the…
According to a story from Biotech 365, the biopharmaceutical company Deciphera Pharmaceuticals has recently announced that the company's drug ripretinib (marketed as QINLOCK™) has been approved by Health Canada. The…
June 23rd, 2020 will be recognized as Dravet Syndrome Awareness Day, and June is Dravet Syndrome Awareness Month. These events are dedicated to spreading awareness about the disorder among the…
According to a recent article in Parkinson’s News Today, results of an extension study confirm that FDA approved Nuplazid (pimavanserin) reduces the severity of delusions and hallucinations in Parkinson’s disease…
“The allergist I have here in town thinks I am *overreacting*. You mean, overreacting when my neighbors next door are cooking their meat on the grill and when I walk…
There is now a new version of the Neupro patch coming! This generic version was created by Vektor Pharma. Vektor concentrates on transdermal systems both through patches on the skin and…
International Nonalcoholic Steatohepatitis (NASH) Day takes place on June 12th every year. This year, a 4 part podcast series was released by NASHNET as part of the continued effort to spread…
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