According to a recent press release from Albireo Pharma, the first participant has enrolled in the BOLD trial. The BOLD trial, which stands for Biliary atresia and the use…
In the early 1990s, Dean Kamen was at the mall when he came up with an idea. After seeing a man in a wheelchair struggle to be noticed by…
According to a story from Parkinson's News Today, a recent study has found a new connection between two different features that appear in Parkinson's disease. These features are lysosomal dysfunction…
According to a story from Korea Biomedical Review, Seoul National University Hospital (SNUH) in South Korea has just announced recently that the process of recruiting patients for the National Bio…
Alpha-synuclein cause damage to mitochondria in patients with Parkinson's disease. These researchers wanted to see if they could see the membrane changes fostered by the alpha-synuclein. The examination of such…
While the world is waiting for a vaccine to prevent, mitigate, or cure COVID-19, the investigational drug remdesivir continues to show promise. The FDA recently gave it Emergency Use…
According to a story from Buzzfeed News, a recent test of an experimental COVID-19 vaccine being developed by Moderna Therapeutics demonstrated that it was able to produce antibodies in all…
As many of us know, funding is a crucial part of medical research and innovation, particularly within the rare disease realm. Recently, the Lupus Research Alliance (LRA), in conjunction…
In 2014, Ki’tay D. Davidson passed away at the age of 22. A black, transgender activist, Ki'tay also used his voice to amplify the experiences and stories of people…
Altogether, there are many foods that promote your health, provide protection against disease, and improve bodily function. According to researchers, there is one that we should be paying more…
The Plasmodium vivax (P. vivax) parasite commonly leads to malaria infection. In fact, around 7.5 million malaria cases result from the parasite. But the tricky part about P. vivax…
The National Institutes of Health (NIH) recently published the results of studies based on a controversy that has remained unresolved for decades. The ISCHEMIA study is not only the…
Living with a rare disease can come with some difficulties, whether those are physical, mental, or financial. It is estimated that 30 million Americans live with a rare disease, a…
ChemoCentryx has just announced that they have submitted their New Drug Application to the FDA for a novel ANCA-associated vasculitis therapy. It is called avacopan and it's finally something non-steroidal.…
According to a study on biorxiv.org, a method called intranasal mechanical stimulation (INMES) appeared effective in reducing symptoms associated with myalgic encephalomyelitis (also called chronic fatigue syndrome) by around 30…
As reported in Parkinson's News Today, three nurses have been awarded $10,000 by The Parkinson’s Foundation to carry out local projects for Parkinson’s patients to better their experience. Each of…
According to a story from PR Newswire, new international treatment recommendation guidelines have recently been updated for nontuberculous mycobacterial (NTM) lung disease. The update pertains to a variant known as Mycobacterium…
According to a story from meaction.net, Dr. Anthony Fauci was recently asked a question about what was being done to address so-called COVID-19 "long haulers," and their potential risk of…
By Lauren Thayer from In The Cloud Copy Nonalcoholic fatty liver disease or NAFLD is a term used to describe a range of conditions in which a patient’s liver has…
By Danielle Bradshaw from In The Cloud Copy The Lancet Psychiatry has published a review stating that although there have been signs demonstrating that delirium may be a common symptom…
According to an article in Globe NewsWire, Onconova Therapeutics, a biopharmaceutical company currently focusing on myelodysplastic syndromes, recently announced results of its Phase 1 study of oral rigosertib in…
By Lauren Thayer from In The Cloud Copy Tourette syndrome (TS) is a neurological disorder that is characterized by involuntary, repetitive movements and vocalizations. These movements and vocalizations are called…
By Lauren Thayer from In The Cloud Copy Fetal alcohol spectrum disorders or FASDs are a group of conditions that can affect a child both physically as well as behaviorally. …
By Lauren Taylor from In The Cloud Copy Biogen announced new data from the NURTURE trial of pre-symptomatic patients with spinal muscular atrophy (SMA). SMA is a rare, autosomal recessive…
According to a story from keloland.com, Westin Cuka, age six, was first diagnosed with neurofibromatosis, a rare disorder, three years ago. Since then, the family has traveled on multiple occasions…
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