Editor's Note: This article was shared with us by Jo Kaur. To see it in its original format, please click here. Riaan Singh Digeorge, age 6, of New York…
As reported on PharmaBiz, Qiagen has received US Food and Drug Administration (FDA) clearance for its QIAstat-Dx BCID GPF Plus AMR Panel, marking the company's entry into the US bloodstream…
As reported on MedIndia, England is set to introduce nationwide newborn screening for spinal muscular atrophy (SMA) in October 2027, a move designed to accelerate diagnosis and enable earlier treatment…
Sibeprenlimab-szsi (VOYXACT) slowed estimated glomerular filtration rate decline versus placebo over 24 months in adult patients with primary IgA nephropathy, according to Phase 3 VISIONARY results announced by Otsuka. Otsuka…
My name is Stephen Savage. I'm happy to say I'm a cancer survivor. I was diagnosed in February, 2019 with a form of adenocarcinoma: esophageal cancer of the lower sphincter.…
As reported of The Manila Times, Health Canada has granted priority review to Chiesi Global Rare Diseases’ new drug submission for FILSUVEZ® (birch triterpenes) topical gel, proposed for treating wounds…
As reported on Fierce Biotech, Silence Therapeutics reported positive phase 2 findings for divesiran, an investigational small interfering RNA (siRNA) treatment for polycythemia vera (PV), a rare blood cancer marked…
As reported on Drugs, Scholar Rock says the US Food and Drug Administration’s review of its biologics license application for apitegromab, an investigational treatment for spinal muscular atrophy (SMA), remains…
Last year, I came down with a severe autoimmune disorder. It came out of nowhere. And it was bad. I was hospitalized three times over the course of a few…
Editor's Note: We are honored to share this story from our friends at CURE SYNGAP. To see this article in its original format, please click here. Porter is one of Jansen’s…
It was 2013, I was 21 years old, studying abroad in Italy, living the semester every college student dreams about. Then I woke up one morning and my body was…
New research presented by Teva Pharmaceuticals at Psych Congress Elevate 2026, and reported on PharmaBiz, adds to the growing body of evidence supporting the use of Austedo (deutetrabenazine) and Austedo…
Living with dystonia, or any chronic condition, places the nervous system under continuous pressure and strain. When symptoms are unpredictable or uncomfortable, the brain learns to stay on high alert, anticipating…
New Treatment Strategy May Eliminate Need for Immediate Organ Removal As reported on Bioengineer, groundbreaking clinical investigation led by researchers at Mayo Clinic suggests that an innovative intravesical immunological agent…
Editor's Note: The following recipe was written and shared with us by our friend Julie, the Cancer Dietitian. I cannot tell you how many people express their amazement and surprise…
New Research Reveals Protective Link Between Routine Immunizations and Uveitis Prevention A comprehensive analysis of patient health records reported on Medscape has uncovered a promising connection: individuals who receive standard…
Editor's Note: The following patient story was submitted to us by Daniel S.—an animal lover, sports fan, and former IIH patient. When you think about shunts, where do you imagine…
As reported on MedScape, gradually extending the interval between belimumab doses may allow carefully selected patients with systemic lupus erythematosus (SLE) in long-term remission to reduce treatment exposure (and in…
As reported on PR Newswire, the US Food and Drug Administration has granted Breakthrough Therapy designation to Kowa’s investigational therapy K-808 (pemafibrate) for primary biliary cholangitis (PBC), the company announced.…
As reported on The ASCO Post, perioperative treatment with enfortumab vedotin-ejfv plus pembrolizumab resulted in superior event-free survival, overall survival, and pathologic response rates compared with neoadjuvant cisplatin/gemcitabine in cisplatin-eligible…
As reported by the BBC, the Ebola outbreak in DR Congo was declared in May 2026 and is now the second worst on record with officials estimating that the death…
Editor's Note: The following article was originally written by Dr. Linda Bluestein. Linda Bluestein, MD, is a board-certified anesthesiologist and internationally recognized expert in hypermobility disorders, integrative pain medicine, and…
As reported on Gizmodo, Samsung has announced that its Galaxy Ring will soon support an FDA-cleared sleep apnea risk detection feature, making it the first smart ring to offer a…
Editor's Note: The following patient story was submitted to us by Christoph Muth, a 52-year-old German man currently residing in Thailand. I am living with a very rare, highly complex,…
As reported by The Manila Times, Axsome Therapeutics has announced the initiation of its Phase 3 CLARITY clinical trial evaluating solriamfetol as a potential treatment for adults with major depressive…
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