According to a story from medicalxpress.com, a team of scientists at the University of Massachusetts Medical School have successfully developed a strategy for editing genes that could be used to…
According to a story from mirror.co.uk, Vanessa Riddle, who had the rare cancer neuroblastoma, recently died after defying her cancer for almost a decade. She passed on June 1st, with…
According to a story from abc.net.au, a team of Australian scientists have developed a technique for delivering radiation therapy that could enhance both the potency and safety of treatment. This…
According to a story from the St. Helens Star, Amanda Sackville-Wiggins was diagnosed with hepatocellular carcinoma, a rare type of liver cancer, just after her 21st birthday. The cancer was…
According to a story from BioPortfolio, the U.S. Food and Drug Administration (FDA) has recently approved a new combination therapy for the treating small lymphocytic lymphoma and chronic lymphocytic leukemia…
According to a story from the San Francisco Chronicle, Isabel Bueso's parents were told when she was born that she would not live more than seven years. However, she continued…
According to a story from Tablet Magazine, Emily Kramer-Golinkoff is a 33 year old woman who is living with cystic fibrosis, a rare disorder that primarily affects the lungs. Emily…
According to a story from sciencemag.org, Huntington's disease can often feel like a curse. That's how it felt for Michelle Dardengo as she watched the disease consume her father. At…
According to a story from BioSpace, Martin Pharmaceuticals' Livantra appears to be on something of a roll. Earlier in the year, the drug received Orphan Drug designation for the treating…
According to a story from kentlive.news, Lucy Frost of Tumbridge Wells is doing everything she can in an attempt to get the NHS to provide her son with the medication he…
According to a story from Nevada Public Radio, in the early 1980s, Lisa Iezzoni was a medical student at Harvard University. Around that time she received a diagnosis of multiple…
According to a story from healthnewsdigest.com, an important source of data related to brain cancer has just become widely available to global researchers. This dataset was supported by Georgetown University,…
According to a story from Newsweek, when 25 year old Rebecca Griffiths first knew that her son Reggie, now aged two, was diagnosed with Sanfilippo syndrome, she had to face…
According to a story from thesun.co.uk, Jade Baldwin, 35 had been dealing with mysterious itchiness for years before she sought medical attention for it. While her legs were itchy, there…
According to a story from Newswise, a team of scientists from the St. Jude's Children's Research Hospital have been hard a work conducting an in-depth analysis of a pediatric solid…
According to a story from Financial Buzz, the drug development company Eisai and Merck recently announced that their cancer drug lenvatinib, marketed as LENVIMA,® has gained marketing approval from the…
According to a story from hemophilia.org, the drug developer uniQure recently announced that the first patient had been dosed in the company's Phase IIb clinical trial. This trial is testing…
According to a story from the Newham Recorder, a three year old girl named Isla Caton's neuroblastoma has relapsed for the second time. Despite the bad news, her mother Nicola…
According to a story from Charcot-Marie-Tooth News, a recent study has managed to identify new clinical evaluations that will allow doctors to more effectively monitor the condition of patients with…
According to a story from EurakAlert!, a group of researchers from the University of Pennsylvania School of Medicine have achieved a major breakthrough for idiopathic pulmonary fibrosis research that will…
According to a story from OncLive, the results of a Phase II trial for an experimental drug called SL-401 showed that the product could be a potentially effective treatment for…
According to a story from Morningstar, the company Alexion Pharmaceuticals recently announced that the U.S. Food and Drug Administration (FDA) has agreed to review their Biologics Licensing Application for their…
According to a story from Globe Newswire, the biotechnology company Wave Life Sciences recently announced that its investigational product WVE-210201 has received both Rare Pediatric disease designation and Orphan Drug…
According to a story from USA Today, despite numerous warning letters sent from the US Food and Drug Administration to the offices of doctors and other medical professionals across the…
According to a story from Deseret News, sarcoma patients at the Huntsman Cancer Institute are planting sunflowers as a way to spread awareness about sarcoma, a rare and aggressive form…
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