According to a story from The Daily Telegraph, Huon May was diagnosed with a serious case of stage 4 neuroblastoma when he was just ten weeks old. The cancer was…
According to a story from PR Newswire, the Hereditary Neuropathy Foundation (HNF) recently announced that it will be conducting a meeting with the US Food and Drug Administration (FDA). This…
According to a story from The Chicago Tribune, Darnesha Bankston, age 23, was rushed to the hospital just before Christmas last year with a bunch of severe, life threatening symptoms.…
According to a story from Euroinvestor, the biotechnology company argenx recently announced that it has gotten correspondence from Japan's Pharmaceuticals and Medical Devices Agency (PMDA) in regards to the design…
According to a story from Shawnee Mission Post, the nonprofit organization RareKC is working to support people with rare diseases that are living the Kansas City area. When living with…
According to a story from Oncology Times, a recent study indicates that the PARP inhibitor drug talazoparib could be an effective treatment option for patients with advanced, HER-2 negative, BRCA…
According to a story from Business Wire, the therapeutics company Alnylam Pharmaceuticals recently announced that the company's drug patisiran has gained approval from the European Commission. Patisiran was approved for…
According to a story from statnews.com, Dr. Julia Brody, who heads the Silent Spring Institute located in Newton, Massachusetts, says that her laboratory has always allowed patients and study participants…
According to a story from the Santa Cruz Sentinel, the earliest results from a critical gene editing study could offer some encouragement for those hoping to treat rare genetic diseases…
The biotechnology company Synlogic announced positive data from its most recent Phase 1/2a clinical trial of its experimental product SYNB1618. This trial did not test the therapeutic action of the…
According to a story from sectorpublishingintelligence.co.uk, a study from the Fraser Institute suggests that the Canadian government's initiative to more closely control the pricing of drugs could place access to…
According to a story from The Rheumatologist, rheumatologists, as specialists in autoimmune disease that can affect multiple body systems, are in a key position to diagnose and treat vasculitis. In…
According to a story from Sunmag, the notorious brain cancer glioblastoma recently claimed the life of a well known figure in public life: Senator John McCain. He was 81 years…
According to a story from medicinenet.com, a recent study found that women on Medicare are not getting genetic tests for BRCA mutations that could lead to ovarian cancer and breast…
According to a story from FiercePharma, the US Food and Drug Administration (FDA) has recently ordered a total of 13 different diabetes drugs to begin carrying warning labels about the…
According to a story from Morningstar, Richard Rendina and his family are no strangers to the challenges and tragedy that can come with a cancer diagnosis. Bruce Redina, for example…
According to a story from prnewswire.com, the drug Cablivi, also known as caplacizumab, has been granted marketing authorization by the European Commission. Cablivi is meant to treat acquired thrombotic thrombocytopenic…
According to a story from uk.news.yahoo.com, Sammy Basso is 22 years old, and for him, it is a miracle. That is because Sammy is living with the rare genetic disorder…
According to a story from Hematology Times, a recent phase 2 study found that a three-part combination treatment could be a valuable treatment option for patients with chronic lymphocytic leukemia.…
According to a story from Multiple Sclerosis News Today, a recent case report suggests that switching from the immunotherapy drug Gilenya to another immunotherapy called Lemtrada could cause a severe…
According to a story from Newswise, the results of a phase 3 clinical trial suggest that the medication tafamidis could substantially reduce the risk of hospitalization or death for patients…
According to a story from journals.lww.com, a recent study investigates the beneficial impact of a thymectomy operation for patients with myasthenia gravis. This procedure has been a common approach for…
According to a story from BioSpace, the gene therapy company Reflection Biotechnologies Ltd. recently announced that the US Food and Drug Administration (FDA) has given Orphan Drug designation to its…
According to a story from Medpage Today, a recent study found that the drug Avapro, which is commonly used to treat high blood pressure, could also slow down the dilation…
According to a story from hms.harvard.edu, a recent study is revealing new information about the connection between aging and neurodegenerative disorders, such as Parkinson's disease, dementia, and amyotrophic lateral sclerosis.…
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