According to a story from statnews.com, Dr. Julia Brody, who heads the Silent Spring Institute located in Newton, Massachusetts, says that her laboratory has always allowed patients and study participants…
According to a story from the Santa Cruz Sentinel, the earliest results from a critical gene editing study could offer some encouragement for those hoping to treat rare genetic diseases…
The biotechnology company Synlogic announced positive data from its most recent Phase 1/2a clinical trial of its experimental product SYNB1618. This trial did not test the therapeutic action of the…
According to a story from sectorpublishingintelligence.co.uk, a study from the Fraser Institute suggests that the Canadian government's initiative to more closely control the pricing of drugs could place access to…
According to a story from The Rheumatologist, rheumatologists, as specialists in autoimmune disease that can affect multiple body systems, are in a key position to diagnose and treat vasculitis. In…
According to a story from Sunmag, the notorious brain cancer glioblastoma recently claimed the life of a well known figure in public life: Senator John McCain. He was 81 years…
According to a story from medicinenet.com, a recent study found that women on Medicare are not getting genetic tests for BRCA mutations that could lead to ovarian cancer and breast…
According to a story from FiercePharma, the US Food and Drug Administration (FDA) has recently ordered a total of 13 different diabetes drugs to begin carrying warning labels about the…
According to a story from Morningstar, Richard Rendina and his family are no strangers to the challenges and tragedy that can come with a cancer diagnosis. Bruce Redina, for example…
According to a story from prnewswire.com, the drug Cablivi, also known as caplacizumab, has been granted marketing authorization by the European Commission. Cablivi is meant to treat acquired thrombotic thrombocytopenic…
According to a story from uk.news.yahoo.com, Sammy Basso is 22 years old, and for him, it is a miracle. That is because Sammy is living with the rare genetic disorder…
According to a story from Hematology Times, a recent phase 2 study found that a three-part combination treatment could be a valuable treatment option for patients with chronic lymphocytic leukemia.…
According to a story from Multiple Sclerosis News Today, a recent case report suggests that switching from the immunotherapy drug Gilenya to another immunotherapy called Lemtrada could cause a severe…
According to a story from Newswise, the results of a phase 3 clinical trial suggest that the medication tafamidis could substantially reduce the risk of hospitalization or death for patients…
According to a story from journals.lww.com, a recent study investigates the beneficial impact of a thymectomy operation for patients with myasthenia gravis. This procedure has been a common approach for…
According to a story from BioSpace, the gene therapy company Reflection Biotechnologies Ltd. recently announced that the US Food and Drug Administration (FDA) has given Orphan Drug designation to its…
According to a story from Medpage Today, a recent study found that the drug Avapro, which is commonly used to treat high blood pressure, could also slow down the dilation…
According to a story from hms.harvard.edu, a recent study is revealing new information about the connection between aging and neurodegenerative disorders, such as Parkinson's disease, dementia, and amyotrophic lateral sclerosis.…
According to a story from globenewswire.com, the pharmaceutical company Novartis recently announced that its CAR-T cell therapy drug Kymriah recently gained approval from the European Commission. The drug was approved…
According to a story from Akcea Therapeutics, the company recently received a reply from the US Food and Drug Administration (FDA) in regards to their New Drug Application for WAYLIVRA…
A recent study published in the journal Nature Communications highlights a potential therapy for the treatment of muscular dytrophies and other diseases linked to mutations of the FKRP gene. In the study, the…
According to a story from BioSpace, the biopharmaceutical company AbbVie recently announced that the US Food and Drug Administration (FDA) has approved a new combination treatment for Waldenstrom's macroglobulinemia (WM).…
According to a story from globnewswire.com, the gene therapy company Adverum Biotechnologies recently announced that the US Food and Drug Administration (FDA) has granted them Orphan Drug designation for their…
According to a story from Medical Xpress, a team of scientists from Michigan State University have managed to reveal the manner in which a genetic malfunction can lead to the…
According to a story from BioSpace, the US Food and Drug Administration (FDA) recently approved the drug Oxervate (cenegermin). This treatment is the first FDA approved therapy for the rare…
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