Gastroschisis Study Cincinnati Children’s Medical Center, Texas Children’s Hospital, and Avery’s Angels are working together to try to learn more about the long-term gastrointestinal issues that people born with gastroschisis…
According to a story from Benzinga, the pharmaceutical company BioCryst Pharmaceuticals, Inc., recently announced that its investigational product BCX7353 has been granted Fast Track Designation from the FDA for the…
According to a story from MPR News, Rae Baylark, who is the founder and current president of the Sickle Cell Foundation of Minnesota, felt like she had nowhere to seek…
According to a story from the pharmaceutical company Takeda, the company recently released the results from its clinical trial testing an experimental subcutaneous formula of the drug vedolizumab. The drug…
According to a story from Beyond the Dish, a new experimental treatment for spinocerebellar ataxia was given the go-ahead from the U.S. Food and Drug Administration for testing. The investigational…
According to a story from BioPortfolio, the company Mologic Ltd recently announced that its clinical trial to test HeadsUp, its urine-based diagnostic tool, is starting. The clinical trial will specifically…
According to a story from Buffalo News, Brett Perla was graduating high school when he first starting to experience symptoms of a rare condition of the cornea called keratoconus. This…
According to a story from PR Newswire, the U.S. Food and Drug Administration had approved the New Drug Application for an innovative new delivery system for Remodulin, a therapy that…
According to a story from philly.com, four year old Ethan Lieber of the Roxborough neighborhood in Philadelphia is one of just 500 people in the US with Hunter syndrome. This…
According to a story from the FH Foundation, the non-profit organization has released a vital consensus statement regarding the diagnosis of familial hypercholesterolemia, which is the most prevalent genetic cause…
According to a story from WebMD, a recent study concludes that the rates of diagnosis for thyroid cancer have been steadily increasing recently, and that it is over treated in…
According to a story from cbc.ca, Cole Pringle is a 31-year-old man from Regina, Saskatchewan with spinal muscular atrophy, a debilitating illness that severely affects his mobility. He was diagnosed…
According to a story from HSC News, Dr. Peter Kuhn from the University of South Carolina (USC) is developing a navigational tool that aims to personalize treatment based on a…
According to a story from pcmag.com, the pharmaceutical company GlaxoSmithKline (GSK) has recently partnered with 23andMe as part of a four year long agreement that will grant the company exclusive…
According to a story from The Sun, Alex was just two months old when he first experienced symptoms of xeroderma pigmentosum. His parents took him out to the park and…
According to a story from rdmag.com, researchers from the University of Toronto have discovered a critical mechanism that helps facilitate the normal DNA repair process. This mechanism could have implications…
According to a story from Pulmonary Hypertension News, It has been three years since Miloš Lazić had is first encounter with pulmonary arterial hypertension. As an active member of Serbia's…
According to a story from Physician's Weekly, a recent study found that small amounts of invisible blood in stool increases the possibility of early death from other causes. The study…
According to a story from KVIA, the University Medical Center at El Paso, Texas, is offering an innovative "hot" chemotherapy treatment that has the potential to treat a variety of…
According to a story from Science Daily, researchers have discovered a mechanism that drives the development of renal cell carcinoma. This mechanism could lead to new therapeutic approaches that take…
According to a story from the Sydney Morning Herald, Hayley Wyatt appeared to be calling for her mother in her final moments, but there was nothing anyone in her family…
According to a story from globenewswire.com, the company Progenic Pharmaceuticals recently reported the the U.S. Food and Drug Administration has recently approved the company's product iobenguane I 131 (AZEDRA). This…
According to a story from publicnow.com, a recent study suggests that it is possible for pancreatic cancer to be diagnosed with a breath test. The discovery could allow for this…
According to a story from Charcot-Marie-Tooth News, a recent study suggests that changes in the levels of two proteins in the body could serve as biomarkers to indicate the progression…
According to a story from MIT Technology Review, it was 2011 when Sonia Vallabh received the results of a genetic test that showed that she had the genetic mutation responsible…
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